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Exon 44 skipping in Duchenne muscular dystrophy: NS-089/NCNP-02, a dual-targeting antisense oligonucleotide Watanabe, Naoki; Tone, Yuichiro; Nagata, Tetsuya; Masuda, Satoru; Saito, Takashi; Motohashi, Norio; Takagaki, Kazuchika; Aoki, Yoshitsugu; Takeda, Shin ' ichi Share Save
Large Maf transcription factor family is a major regulator of fast type IIb myofiber determination Sadaki, Shunya; Fujita, Ryo; Hayashi, Takuto; Nakamura, Ayano; Okamura, Yui; Fuseya, Sayaka; Hamada, Michito; Warabi, Eiji; Kuno, Akihiro; Ishii, Akiko; Muratani, Masafumi; Okada, Risa; Shiba, Dai; Kudo, Takashi; Takeda, Shin'ichi; Takahashi, Satoru Share Save
Ubiquitin Ligase Cbl-b Is a Negative Regulator for Insulin-Like Growth Factor 1 Signaling during Muscle Atrophy Caused by Unloading Nakao, Reiko; Hirasaka, Katsuya; Goto, Jumpei; Ishidoh, Kazumi; Yamada, Chiharu; Ohno, Ayako; Okumura, Yuushi; Nonaka, Ikuya; Yasutomo, Koji; Baldwin, Kenneth M.; Kominami, Eiki; Higashibata, Akira; Nagano, Keisuke; Tanaka, Keiji; Yasui, Natsuo; Mills, Edward M.; Takeda, Shin'ichi; Nikawa, Takeshi Share Save
Full-length human dystrophin on human artificial chromosome compensates for mouse dystrophin deficiency in a Duchenne muscular dystrophy mouse model Hiramuki, Yosuke; Abe, Satoshi; Uno, Narumi; Kazuki, Kanako; Takata, Shuta; Miyamoto, Hitomaru; Takayama, Haruka; Morimoto, Kayoko; Takehara, Shoko; Osaki, Mitsuhiko; Tanihata, Jun; Takeda, Shin'ichi; Tomizuka, Kazuma; Oshimura, Mitsuo; Kazuki, Yasuhiro Share Save
Brain Dp140 alters glutamatergic transmission and social behaviour in the mdx52 mouse model of Duchenne muscular dystrophy Hashimoto, Yasumasa; Kuniishi, Hiroshi; Sakai, Kazuhisa; Fukushima, Yuta; Du, Xuan; Yamashiro, Kunihiko; Hori, Kei; Imamura, Michihiro; Hoshino, Mikio; Yamada, Mitsuhiko; Araki, Toshiyuki; Sakagami, Hiroyuki; Takeda, Shinichi; Itaka, Keiji; Ichinohe, Noritaka; Muntoni, Francesco; Sekiguchi, Masayuki; Aoki, Yoshitsugu Share Save
A new mouse model of Ehlers-Danlos syndrome generated using CRISPR/Cas9-mediated genomic editing Nitahara-Kasahara, Yuko; Mizumoto, Shuji; Inoue, Yukiko U.; Saka, Shota; Posadas-Herrera, Guillermo; Nakamura-Takahashi, Aki; Takahashi, Yuki; Hashimoto, Ayana; Konishi, Kohei; Miyata, Shinji; Masuda, Chiaki; Matsumoto, Emi; Maruoka, Yasunobu; Yoshizawa, Takahiro; Tanase, Toshiki; Inoue, Takayoshi; Yamada, Shuhei; Nomura, Yoshihiro; Takeda, Shin'ichi; Watanabe, Atsushi; Kosho, Tomoki; Okada, Takashi Share Save
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Pharmacological activation of SERCA ameliorates dystrophic phenotypes in dystrophin-deficient mdx mice Nogami, Ken'ichiro; Maruyama, Yusuke; Sakai-Takemura, Fusako; Motohashi, Norio; Elhussieny, Ahmed; Imamura, Michihiro; Miyashita, Satoshi; Ogawa, Megumu; Noguchi, Satoru; Tamura, Yuki; Kira, Jun-ichi; Aoki, Yoshitsugu; Takeda, Shin'ichi; Miyagoe-Suzuki, Yuko Share Save
Immortalized Canine Dystrophic Myoblast Cell Lines for Development of Peptide-Conjugated Splice-Switching Oligonucleotides Tone, Yuichiro; Mamchaoui, Kamel; Tsoumpra, Maria K.; Hashimoto, Yasumasa; Terada, Reiko; Maruyama, Rika; Gait, Michael J.; Arzumanov, Andrey A.; McClorey, Graham; Imamura, Michihiro; Takeda, Shin'ichi; Yokota, Toshifumi; Wood, Matthew J. A.; Mouly, Vincent; Aoki, Yoshitsugu Share Save
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Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study Komaki, Hirofumi; Takeshima, Yasuhiro; Matsumura, Tsuyoshi; Ozasa, Shiro; Funato, Michinori; Takeshita, Eri; Iwata, Yasuyuki; Yajima, Hiroyuki; Egawa, Yoichi; Toramoto, Takuya; Tajima, Masaya; Takeda, Shinichi Share Save
Mutation-independent Proteomic Signatures of Pathological Progression in Murine Models of Duchenne Muscular Dystrophy van Westering, Tirsa L. E.; Johansson, Henrik J.; Hanson, Britt; Coenen-Stass, Anna M. L.; Lomonosova, Yulia; Tanihata, Jun; Motohashi, Norio; Yokota, Toshifumi; Takeda, Shin'ichi; Lehtio, Janne; Wood, Matthew J. A.; EL Andaloussi, Samir; Aoki, Yoshitsugu; Roberts, Thomas C. Share Save
The nSMase2/Smpd3 gene modulates the severity of muscular dystrophy and the emotional stress response in mdx mice Matsuzaka, Yasunari; Tanihata, Jun; Ooshima, Yoshiko; Yamada, Daisuke; Sekiguchi, Masayuki; Miyatake, Shouta; Aoki, Yoshitsugu; Terumitsu, Mika; Yashiro, Ryu; Komaki, Hirofumi; Ishiyama, Akihiko; Oya, Yasushi; Inoue, Yukiko U.; Inoue, Takayoshi; Takeda, Shin'ichi; Hashido, Kazuo Share Save
Novel EGFP reporter cell and mouse models for sensitive imaging and quantification of exon skipping Hara, Yuko; Mizobe, Yoshitaka; Inoue, Yukiko U.; Hashimoto, Yasumasa; Motohashi, Norio; Masaki, Yoshiaki; Seio, Kohji; Takeda, Shin'ichi; Nagata, Tetsuya; Wood, Matthew J. A.; Inoue, Takayoshi; Aoki, Yoshitsugu Share Save