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PIONEERING QUAD-TARGETING CAR T CELL THERAPY IN PEDIATRIC CNS TUMORS - ANALYSIS FROM THE FIRST-IN-HUMAN PHASE 1 TRIAL BRAINCHILD-04 Ronsley, Rebecca; Seidel, Kristy; Narayanaswamy, Prabha; Pattabhi, Sowmya; Wendler, Jason; Rawlings-Rhea, Stephanie; Huang, Wenjun; Crotty, Erin; Leary, Sarah; Lee, Amy; Park, Julie; Jensen, Michael; Vitanza, Nicholas Share Save
Locoregional B7-H3 CAR-T cells for relapsed/refractory CNS tumors: preliminary clinical experience of the Loc3CAR trial Bertrand, Kelsey; Hanzlik, Emily; Chiang, Jason; Pinto, Soniya; Selukar, Subodh; Kosteka, Anna; Smith, Kyle; Han, Katie; Ibanez, Jorge; Tlais, Dana; Orr, Brent; Langfitt, Deanna; Metais, Jean-Yves; Lockey, Timothy; Willis, Catherine; Fazio, Frank; Shanmugmam, Raghu; Tian, Liqing; Walhart, Tara; Wang, Yu; Allmon, Patricia; Perry, Scott; Schell, Sarah; Adams, Polly; Ward, Meghan; Meehl, Michaela; Akel, Salem; Poston, Leigh; Bag, Asim; Mack, Stephen; Klimo, Paul; Gajjar, Amar; Thomas, Paul; Crawford, Jeremy; Robinson, Giles; Park, Julie; Northcott, Paul; Gottschalk, Stephen; Krenciute, Giedre; Derenzo, Christopher Share Save
Tumor inflammation-associated neurotoxicities for patients treated with intracranial B7-H3-CAR T cells on a phase I clinical trial Hanzlik, Emily M.; Bertrand, Kelsey C.; Chiang, Jason; Pinto, Soniya; Khan, Raja B.; Solanki, Arun; Selukar, Subodh; Wang, Yu; Bakare, Deborah; Swartz, Kate; Gajjar, Amar; Robinson, Giles W.; Park, Julie R.; Gottschalk, Stephen; Krenciute, Giedre; Derenzo, Christopher Share Save
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Tumor inflammation-associated neurotoxicity in children with diffuse intrinsic pontine glioma receiving B7-H3-targeting CAR T cells on BrainChild-03 Ronsley, Rebecca; Choe, Michelle; Wright, Jason; Seidel, Kristy; Lee, Amy; Wendler, Jason; Annesley, Colleen; Jensen, Michael C.; Park, Julie R.; Vitanza, Nicholas A.; Gust, Juliane Share Save
International neuroblastoma risk group consortium: a model of networking for rare cancers Susan L Cohn, MD; Wendy B London, PhD; Gudrun Schleiermacher, MD, PhD; Lucas Moreno, MD, PhD; Inge M Ambros, PhD; Peter F Ambros, PhD; Rochelle Bagatell, MD; Maja Beck Popovic, MD; Klaus Hermann Beiske, MD, PhD; Frank Berthold, MD; Suzi Birz, MScMI; Hervé J Brisse, MD; Garrett M Brodeur, MD; Penelope R Brock, MD; Susan Burchill, PhD; Angelika Eggert, MD; Sara M Federico, MD; Matthias Fischer, PhD; Brian T Furner, MS; Barbara Hero, MD; David Machin, PhD; Takehiko Kamijo, MD; Katherine K Matthay, MD; Akira Nakagawara, MD, PhD; Arlene Naranjo, PhD; Ulrike Pötschger, PhD; Dominique Valteau-Couanet, MD; Michael T Watkins, PhD; Meredith S Irwin, MD; Samuel L Volchenboum, MD, PhD; Julie R Park, MD; Andrew D J Pearson, MD; null Share Save
Locoregional infusion of EGFR806-CAR T cells for recurrent or refractory pediatric CNS tumors: Results of the completed BrainChild02 phase 1 clinical trial Gust, Juliane; Cole, Bonnie L.; Ronsley, Rebecca; Wilson, Ashley L.; Seidel, Kristy; Wendler, Jason; Pattabhi, Sowmya; Brown, Christopher; Rawlings-Rhea, Stephanie D.; Shtanukhina, Nadezhda; Browd, Samuel R.; Hauptman, Jason S.; Lee, Amy; Ojemann, Jeffrey G.; Crotty, Erin E.; Leary, Sarah E. S.; Perez, Francisco A.; Wright, Jason N.; Albert, Catherine M.; Pinto, Navin; Gardner, Rebecca A.; Vitanza, Nicholas A.; Jensen, Michael C.; Park, Julie R. Share Save
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A phase 1 dose-escalation study of LY3295668 erbumine as monotherapy and in combination with topotecan and cyclophosphamide in children with relapsed/refractory neuroblastoma DuBois, Steven G.; Ogawa, Chitose; Moreno, Lucas; Mosse, Yael P.; Fischer, Matthias; Ryan, Anne L.; Vo, Kieuhoa T.; De Wilde, Bram; Rubio-San-Simon, Alba; Macy, Margaret E.; Howell, Lisa; Shusterman, Suzanne; Corradini, Nadege; Luksch, Roberto; Aerts, Isabelle; Foster, Jennifer H.; Weiss, Brian D.; Karthik, Chandrasekhar Pamidipati; Yuen, Eunice; Avsar, Emin; Park, Julie R.; Marachelian, Araz Share Save
LOCOREGIONAL ADMINISTRATION OF B7-H3-CAR T CELLS EXPRESSING 41BB LIGAND FOR PEDIATRIC PATIENTS WITH PRIMARY CNS TUMORS: PRELIMINARY RESULTS FROM A PHASE I STUDY Bertrand, Kelsey C.; Kostecka, Anna; Smith, Kyle; Han, Katie; Chiang, Jason; Pinto, Soniya; Tlais, Dana; Selukar, Subodh; Orr, Brent; Hanzlik, Emily; Langfitt, Deanna; Metais, Jean-Yves; Lockey, Timothy; Willis, Catherine; Fazio, Frank; Shanmugam, Raghu; Tian, Liqing; Walhart, Tara; Wang, Yu; Allmon, Patricia; Perry, Scott; Schell, Sarah; Adams, Polly; Ward, Meghan B.; Meehl, Michaela; Akel, Salem; Poston, Leigh; Bag, Asim; Mack, Stephen C.; Leggas, Markos; Klimo, Paul; Gajjar, Amar; Thomas, Paul; Robinson, Giles W.; Park, Julie R.; Crawford, Jeremy Chase; Gottschalk, Stephen; Northcott, Paul A.; Krenciute, Giedre; Derenzo, Christopher Share Save
PIONEERING QUAD-TARGETING CAR T CELL THERAPY IN PEDIATRIC CNS TUMORS - ANALYSIS FROM THE INITIAL PATIENTS TREATED ON THE FIRST-IN-HUMAN PHASE 1 TRIAL BRAINCHILD-04 Ronsley, Rebecca; Seidel, Kristy; Narayanaswamy, Prabha; Pattabhi, Sowmya; Wendler, Jason; Ho, On; Rawlings-Rhea, Stephanie; Gust, Juliane; Huang, Wenjun; Crotty, Erin; Leary, Sarah; Runco, Daniel; Hauptman, Jason; Gardner, Rebecca; Park, Julie; Annesley, Colleen; Jensen, Michael; Vitanza, Nicholas Share Save
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Perspectives of pediatric oncologists on referral for CAR-T therapy: a mixed methods pilot study Hall, Anurekha G.; Duenas, Devan M.; Voutsinas, Jenna; Wu, Qian; Lamble, Adam J.; Gruber, Elizabeth; Wilfond, Benjamin; Park, Julie R.; Agrawal, Anurag K.; Marron, Jonathan M. Share Save
INTRAVENTRICULAR B7-H3 CAR T CELLS FOR DIFFUSE INTRINSIC PONTINE GLIOMA: SAFETY AND EFFICACY REPORT FROM THE COMPLETED PHASE 1 TRIAL BRAINCHILD-03 Vitanza, Nicholas A.; Ronsley, Rebecca; Huang, Wenjuan; Seidel, Kristy; Thomsen, Alison; Gust, Juliane; Hauptman, Jason; Choe, Michlle; Crotty, Erin; Leary, Sarah; Gustafson, Joshua A.; Gardner, Rebecca A.; Pattabhi, Sowmya; Wendler, Jason; Ho, On; Annesley, Colleen; Park, Julie R.; Jensen, Michael C. Share Save
TUMOR INFLAMMATION-ASSOCIATED NEUROTOXICITY (TIAN): A TOXICITY SYNDROME IN PATIENTS TREATED WITH IMMUNOTHERAPY FOR CENTRAL NERVOUS SYSTEM TUMORS Mahdi, Jasia; Dietrich, Jorg; Straathof, Karin; Roddie, Claire; Scott, Brian J.; Davidson, Tom Belle; Prolo, Laura; Batchelor, Tracy T.; Campen, Cynthia J.; Davis, Kara L.; Gust, Juliane; Lim, Michael; Majzner, Robbie G.; Park, Julie R.; Partap, Sonia; Ramakrishna, Sneha; Richards, Rebecca; Schultz, Liora; Vitanza, Nicholas A.; Wang, Leo D.; Mackall, Crystal L.; Monje, Michelle Share Save
PIONEERING QUAD-TARGETING CAR T CELL THERAPY IN PEDIATRIC CNS TUMORS - ANALYSIS FROM THE INITIAL PATIENTS TREATED ON THE FIRST-IN-HUMAN PHASE 1 TRIAL BRAINCHILD-04 Ronsley, Rebecca; Choe, Michelle; Seidel, Kristy; Narayanaswamy, Prabha; Pattabhi, Sowmya; Wendler, Jason; Ho, On; Rawlings-Rhea, Stephanie; Gust, Juliane; Huang, Wenjun; Crotty, Erin; Leary, Sarah; Hauptman, Jason; Albert, Catherine M.; Gardner, Rebecca A.; Park, Julie R.; Annesley, Colleen; Jensen, Michael C.; Vitanza, Nicholas A. Share Save
Development of a Safety Surveillance Plan for the Academic Medicine Sponsor Performing First-in-Human Cellular Therapy Clinical Trials: A Report from the Consortium for Pediatric Cellular Immunotherapy Adams, Cheri; Keller, Michael; Michlitsch, Jennifer G.; Aguayo-Hiraldo, Paibel; Chen, Karin; Hossain, Mohammad Z.; Davis, Ann; Park, Julie R.; Verneris, Michael R.; Gardner, Rebecca A. Share Save