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Giuliana Ferrari

Vita-Salute San Raffaele University

51H-index
239Paper Count
1.3WCitation Count
Published Papers 56
Publication Date
Claudio Bordignon
err2026-06-16
err0
PREAI
errAlessandro Aiuti; Chiara Bonini; Fabio Ciceri; Giuliana Ferrari; Fulvio Mavilio; Luigi Naldini
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Iron overload damages mitochondria and induces metabolic rewiring of hematopoietic stem cells towards glycolysis
errBlood
IF23.1
err2026-03-26
err0
errOAAI
errSilvia Sighinolfi; Laura Cassina; Maria Rosa Lidonnici; Stefano Beretta; Davide Stefanoni; Mariangela Storto; Christina Mayerhofer; Trine A Kristiansen; David T Scadden; Ivan Merelli; Alessandra Boletta; Annamaria Aprile; Giuliana Ferrari
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Base editing of β0-thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies
err2025-11-26
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PREAI
errGiulia Hardouin; Pierre Martinucci; Samantha Scaramuzza; Panagiotis Antoniou; Federico Corradi; Alexandra Tachtsidi; Guillaume Corre; Margaux Mombled; Jessika Chermont; Sandra Manceau; Cécile Rouillon; Cécile Masson; Laure Joseph; Isabelle Thuret; Catherine Badens; Sarah Szepetowsky; Eric Allemand; Mario Amendola; Oriana Romano; Giuliana Ferrari; Annarita Miccio
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Immunomodulatory effects of dental pulp stem cells on lymphocytes and monocytes from patients with rheumatoid arthritis
err2025-05-08
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PREAI
errRossi, A.; Ferrari, G.; Galli, V.; Bonacini, M.; Carnevale, G.; Pisciotta, A.; Di Tinco, R.; Catanoso, M.; Brandolino, F.; Galluzzo, C.; Zerbini, A.; Salvarani, C.; Croci, S.
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Removal of innate immune barriers allows efficient transduction of quiescent human hematopoietic stem cells
err2024-01-01
err2
errOAAI
errValeri, Erika; Unali, Giulia; Piras, Francesco; Abou-Alezz, Monah; Pais, Giulia; Benedicenti, Fabrizio; Lidonnici, Maria Rosa; Cuccovillo, Ivan; Castiglioni, Ilaria; Arevalo, Sergio; Spinozzi, Giulio; Merelli, Ivan; Behrendt, Rayk; Oo, Adrian; Kim, Baek; Landau, Nathaniel R.; Ferrari, Giuliana; Montini, Eugenio; Kajaste-Rudnitski, Anna
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A single approach to targeting transferrin receptor 2 corrects iron and erythropoietic defects in murine models of anemia of inflammation and chronic disease
err2023-07-01
err11
PREAI
errOlivari, Violante; Di Modica, Simona Maria; Lidonnici, Maria Rosa; Aghajan, Mariam; Cordero-Sanchez, Celia; Tanzi, Emanuele; Pettinato, Mariateresa; Pagani, Alessia; Tiboni, Francesca; Silvestri, Laura; Guo, Shuling; Ferrari, Giuliana; Nai, Antonella
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Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies
err2023-06-01
err5
errOAAI
errBrusson, Megane; Chalumeau, Anne; Martinucci, Pierre; Romano, Oriana; Felix, Tristan; Poletti, Valentina; Scaramuzza, Samantha; Ramadier, Sophie; Masson, Cecile; Ferrari, Giuliana; Mavilio, Fulvio; Cavazzana, Marina; Amendola, Mario; Miccio, Annarita
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Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia
err2023-05-31
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PREAI
errAprile, Annamaria; Raggi, Laura; Bolamperti, Simona; Villa, Isabella; Storto, Mariangela; Morello, Gaia; Marktel, Sarah; Tripodo, Claudio; Cappellini, Maria Domenica; Motta, Irene; Rubinacci, Alessandro; Ferrari, Giuliana
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Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy
err2023-05-01
err22
errOAAI
errFerrari, Samuele; Valeri, Erika; Conti, Anastasia; Scala, Serena; Aprile, Annamaria; Di Micco, Raffaella; Kajaste-Rudnitski, Anna; Montini, Eugenio; Ferrari, Giuliana; Aiuti, Alessandro; Naldini, Luigi
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Hypomorphic mutation of the TALE gene Prep1 (pKnox1) causes a major reduction of Pbx and Meis proteins and a pleiotropic embryonic phenotype
err2023-03-27
err95
errOAAI
errFerretti, Elisabetta; Villaescusa, J. Carlos; Di Rosa, Patrizia; Fernandez-Diaz, Luis C.; Longobardi, Elena; Mazzieri, Roberta; Miccio, Annarita; Micali, Nicola; Selleri, Licia; Ferrari, Giuliana; Blasi, Francesco
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Assessing and enhancing migration of human myogenic progenitors using directed iPS cell differentiation and advanced tissue modelling
err2022-09-26
err10
errOAAI
errChoi, SungWoo; Ferrari, Giulia; Moyle, Louise A.; Mackinlay, Kirsty; Naouar, Naira; Jalal, Salma; Benedetti, Sara; Wells, Christine; Muntoni, Francesco; Tedesco, Francesco Saverio
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Transferrin receptor 2 (Tfr2) genetic deletion makes transfusion-independent a murine model of transfusion-dependent β-thalassemia
err2022-08-10
err9
errOAAI
errDi Modica, Simona Maria; Tanzi, Emanuele; Olivari, Violante; Lidonnici, Maria Rosa; Pettinato, Mariateresa; Pagani, Alessia; Tiboni, Francesca; Furiosi, Valeria; Silvestri, Laura; Ferrari, Giuliana; Rivella, Stefano; Nai, Antonella
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Targeting the Hematopoietic Stem Cell Niche in β-Thalassemia and Sickle Cell Disease
err2022-05-11
err5
errOAAI
errAprile, Annamaria; Sighinolfi, Silvia; Raggi, Laura; Ferrari, Giuliana
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Investigating the role of dystrophin isoform deficiency in motor function in Duchenne muscular dystrophy
err2022-01-26
err27
errOAAI
errChesshyre, Mary; Ridout, Deborah; Hashimoto, Yasumasa; Ookubo, Yoko; Torelli, Silvia; Maresh, Kate; Ricotti, Valeria; Abbott, Lianne; Gupta, Vandana Ayyar; Main, Marion; Ferrari, Giulia; Kowala, Anna; Lin, Yung-Yao; Tedesco, Francesco Saverio; Scoto, Mariacristina; Baranello, Giovanni; Manzur, Adnan; Aoki, Yoshitsugu; Muntoni, Francesco
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Dystrophin deficiency affects human astrocyte properties andresponse to damage
errGLIA
IF5.1
err2021-11-13
err15
errOAAI
errLange, Jenny; Gillham, Olivia; Alkharji, Reem; Eaton, Simon; Ferrari, Giulia; Madej, Monika; Flower, Michael; Tedesco, Francesco Saverio; Muntoni, Francesco; Ferretti, Patrizia
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Engineering of human induced pluripotent stem cells via human artificial chromosome vectors for cell therapy and disease modeling
err2021-03-01
err11
errOAAI
errKazuki, Yasuhiro; Uno, Narumi; Abe, Satoshi; Kajitani, Naoyo; Kazuki, Kanako; Yakura, Yuwna; Sawada, Chiaki; Takata, Shuta; Sugawara, Masaki; Nagashima, Yuichi; Okada, Akane; Hiratsuka, Masaharu; Osaki, Mitsuhiko; Ferrari, Giulia; Tedesco, Francesco Saverio; Nishikawa, Satoshi; Fukumoto, Ken; Takayanagi, Shin-ichiro; Kunisato, Atsushi; Kaneko, Shin; Oshimura, Mitsuo; Tomizuka, Kazuma
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Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells
err2021-02-26
err55
errOAAI
errPavani, Giulia; Fabiano, Anna; Laurent, Marine; Amor, Fatima; Cantelli, Erika; Chalumeau, Anne; Maule, Giulia; Tachtsidi, Alexandra; Concordet, Jean-Paul; Cereseto, Anna; Mavilio, Fulvio; Ferrari, Giuliana; Miccio, Annarita; Amendola, Mario
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Gene therapy using haematopoietic stem and progenitor cells
err2020-12-10
err160
errOAAI
errFerrari, Giuliana; Thrasher, Adrian J.; Aiuti, Alessandro
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