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Immunomodulatory effects of dental pulp stem cells on lymphocytes and monocytes from patients with rheumatoid arthritis Rossi, A.; Ferrari, G.; Galli, V.; Bonacini, M.; Carnevale, G.; Pisciotta, A.; Di Tinco, R.; Catanoso, M.; Brandolino, F.; Galluzzo, C.; Zerbini, A.; Salvarani, C.; Croci, S. Share Save
Removal of innate immune barriers allows efficient transduction of quiescent human hematopoietic stem cells Valeri, Erika; Unali, Giulia; Piras, Francesco; Abou-Alezz, Monah; Pais, Giulia; Benedicenti, Fabrizio; Lidonnici, Maria Rosa; Cuccovillo, Ivan; Castiglioni, Ilaria; Arevalo, Sergio; Spinozzi, Giulio; Merelli, Ivan; Behrendt, Rayk; Oo, Adrian; Kim, Baek; Landau, Nathaniel R.; Ferrari, Giuliana; Montini, Eugenio; Kajaste-Rudnitski, Anna Share Save
A single approach to targeting transferrin receptor 2 corrects iron and erythropoietic defects in murine models of anemia of inflammation and chronic disease Olivari, Violante; Di Modica, Simona Maria; Lidonnici, Maria Rosa; Aghajan, Mariam; Cordero-Sanchez, Celia; Tanzi, Emanuele; Pettinato, Mariateresa; Pagani, Alessia; Tiboni, Francesca; Silvestri, Laura; Guo, Shuling; Ferrari, Giuliana; Nai, Antonella Share Save
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies Brusson, Megane; Chalumeau, Anne; Martinucci, Pierre; Romano, Oriana; Felix, Tristan; Poletti, Valentina; Scaramuzza, Samantha; Ramadier, Sophie; Masson, Cecile; Ferrari, Giuliana; Mavilio, Fulvio; Cavazzana, Marina; Amendola, Mario; Miccio, Annarita Share Save
Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia Aprile, Annamaria; Raggi, Laura; Bolamperti, Simona; Villa, Isabella; Storto, Mariangela; Morello, Gaia; Marktel, Sarah; Tripodo, Claudio; Cappellini, Maria Domenica; Motta, Irene; Rubinacci, Alessandro; Ferrari, Giuliana Share Save
Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy Ferrari, Samuele; Valeri, Erika; Conti, Anastasia; Scala, Serena; Aprile, Annamaria; Di Micco, Raffaella; Kajaste-Rudnitski, Anna; Montini, Eugenio; Ferrari, Giuliana; Aiuti, Alessandro; Naldini, Luigi Share Save
Hypomorphic mutation of the TALE gene Prep1 (pKnox1) causes a major reduction of Pbx and Meis proteins and a pleiotropic embryonic phenotype Ferretti, Elisabetta; Villaescusa, J. Carlos; Di Rosa, Patrizia; Fernandez-Diaz, Luis C.; Longobardi, Elena; Mazzieri, Roberta; Miccio, Annarita; Micali, Nicola; Selleri, Licia; Ferrari, Giuliana; Blasi, Francesco Share Save
Assessing and enhancing migration of human myogenic progenitors using directed iPS cell differentiation and advanced tissue modelling Choi, SungWoo; Ferrari, Giulia; Moyle, Louise A.; Mackinlay, Kirsty; Naouar, Naira; Jalal, Salma; Benedetti, Sara; Wells, Christine; Muntoni, Francesco; Tedesco, Francesco Saverio Share Save
Transferrin receptor 2 (Tfr2) genetic deletion makes transfusion-independent a murine model of transfusion-dependent β-thalassemia Di Modica, Simona Maria; Tanzi, Emanuele; Olivari, Violante; Lidonnici, Maria Rosa; Pettinato, Mariateresa; Pagani, Alessia; Tiboni, Francesca; Furiosi, Valeria; Silvestri, Laura; Ferrari, Giuliana; Rivella, Stefano; Nai, Antonella Share Save
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Investigating the role of dystrophin isoform deficiency in motor function in Duchenne muscular dystrophy Chesshyre, Mary; Ridout, Deborah; Hashimoto, Yasumasa; Ookubo, Yoko; Torelli, Silvia; Maresh, Kate; Ricotti, Valeria; Abbott, Lianne; Gupta, Vandana Ayyar; Main, Marion; Ferrari, Giulia; Kowala, Anna; Lin, Yung-Yao; Tedesco, Francesco Saverio; Scoto, Mariacristina; Baranello, Giovanni; Manzur, Adnan; Aoki, Yoshitsugu; Muntoni, Francesco Share Save
Dystrophin deficiency affects human astrocyte properties andresponse to damage Lange, Jenny; Gillham, Olivia; Alkharji, Reem; Eaton, Simon; Ferrari, Giulia; Madej, Monika; Flower, Michael; Tedesco, Francesco Saverio; Muntoni, Francesco; Ferretti, Patrizia Share Save
Engineering of human induced pluripotent stem cells via human artificial chromosome vectors for cell therapy and disease modeling Kazuki, Yasuhiro; Uno, Narumi; Abe, Satoshi; Kajitani, Naoyo; Kazuki, Kanako; Yakura, Yuwna; Sawada, Chiaki; Takata, Shuta; Sugawara, Masaki; Nagashima, Yuichi; Okada, Akane; Hiratsuka, Masaharu; Osaki, Mitsuhiko; Ferrari, Giulia; Tedesco, Francesco Saverio; Nishikawa, Satoshi; Fukumoto, Ken; Takayanagi, Shin-ichiro; Kunisato, Atsushi; Kaneko, Shin; Oshimura, Mitsuo; Tomizuka, Kazuma Share Save
Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells Pavani, Giulia; Fabiano, Anna; Laurent, Marine; Amor, Fatima; Cantelli, Erika; Chalumeau, Anne; Maule, Giulia; Tachtsidi, Alexandra; Concordet, Jean-Paul; Cereseto, Anna; Mavilio, Fulvio; Ferrari, Giuliana; Miccio, Annarita; Amendola, Mario Share Save
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