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André Lieber

Medical Genetics

61H-index
328Paper Count
1.3WCitation Count
Published Papers 136
Publication Date
De novo design of miniproteins targeting GPCRs
errNature
IF48.5
err2026-05-21
err0
PREAI
errEdin Muratspahić; David Feldman; David E. Kim; Xiangli Qu; Ana-Maria Bratovianu; Paula Rivera-Sánchez; Jan Hendrik Voss; Emil P. T. Hertz; Mads Jeppesen; Federica Dimitri; Kensuke Sakamoto; Amrita Nallathambi; Pia Peceli; Jianjun Cao; Brian P. Cary; Matthew J. Belousoff; Peter Keov; Phuc N. H. Trinh; Qingchao Chen; Yue Ren; Justyn Fine; Sudha Mishra; Annu Dalal; Shachie Sinha; Ramanuj Banerjee; Manisankar Ganguly; Karthik Varappalayam Karuppusamy; Isaac Sappington; Thomas Schlichthaerle; Jason Z. Zhang; Arvind Pillai; Brian Coventry; Ljubica Mihaljević; Magnus Bauer; Susana Vázquez Torres; Amir Motmaen; Gyu Rie Lee; Long Tran; Xinru Wang; Inna Goreshnik; Dionne K. Vafeados; Justin E. Svendsen; Parisa Hosseinzadeh; Nicolai Lindegaard; Matthäus Brandt; Yann Waltenspühl; Kristine Deibler; Lukas Deweid; Anja Bennett; Jendrik Schöppe; Tiantang Dong; Xiaoli Yan; Luke Oostdyk; William Cao; Lakshmi Anantharaman; Johan J. Weisser; Jesper Frank Bastlund; Christoffer Bundgaard; Ayodeji A. Asuni; Justin G. English; Lance Stewart; Lauren Halloran; Jamie B. Spangler; André Lieber; Arun K. Shukla; Patrick M. Sexton; Bryan L. Roth; Brian E. Krumm; Denise Wootten; Christopher G. Tate; Christoffer Norn; David Baker
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In vivo HSC transduction in humanized mice mediated by novel capsid-modified HDAd vectors
err2025-06-01
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errOAAI
errAphrodite Georgakopoulou; Hongjie Wang; Jiho Kim; Chang Li; André Lieber
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Resolving the chromatin impact of mosaic variants with targeted Fiber-seq
err2024-12-09
err1
errOAAI
errBohaczuk, Stephanie C.; Amador, Zachary J.; Li, Chang; Mallory, Benjamin J.; Swanson, Elliott G.; Ranchalis, Jane; Vollger, Mitchell R.; Munson, Katherine M.; Walsh, Tom; Hamm, Morgan O.; Mao, Yizi; Lieber, Andre; Stergachis, Andrew B.
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Introducing a hemoglobin G-Makassar variant in HSCs by in vivo base editing treats sickle cell disease in mice
err2024-12-01
err1
errOAAI
errLi, Chang; Georgakopoulou, Aphrodite; Paschoudi, Kiriaki; Anderson, Anna K.; Huang, Lishan; Gil, Sucheol; Giannaki, Maria; Vlachaki, Efthymia; Newby, Gregory A.; Liu, David R.; Yannaki, Evangelia; Kiem, Hans-Peter; Lieber, Andre
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A simplified G-CSF-free procedure allows for in vivo HSC gene therapy of sickle cell disease in a mouse model
err2024-07-31
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errOAAI
errLi, Chang; Anderson, Anna K.; Ruminski, Peter; Rettig, Michael; Karpova, Darja; Kiem, Hans-Peter; DiPersio, John F.; Lieber, Andre
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Stable HIV decoy receptor expression after in vivo HSC transduction in mice and NHPs: Safety and efficacy in protection from SHIV (vol 31, pg 1059, 2023)
err2023-04-01
err1
errOAAI
errLi, Chang; Anderson, Anna Kate; Wang, Hongjie; Gil, Sucheol; Kim, Jiho; Huang, Lishan; Germond, Audrey; Baldessari, Audrey; Nelson, Veronica; Bar, Katharine J.; Peterson, Christopher W.; Bui, John; Kiem, Hans-Peter; Lieber, Andre
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Stable HIV decoy receptor expression after in vivo HSC transduction in mice and NHPs: Safety and efficacy in protection from SHIV
err2023-04-01
err3
errOAAI
errLi, Chang; Anderson, Anna Kate; Wang, Hongjie; Gil, Sucheol; Kim, Jiho; Huang, Lishan; Germond, Audrey; Baldessari, Audrey; Nelson, Veronica; Bar, Katharine J.; Peterson, Christopher W.; Bui, John; Kiem, Hans -Peter; Lieber, Andre
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In vivo base editing by a single i.v. vector injection for treatment of hemoglobinopathies
err2022-10-10
err21
errOAAI
errLi, Chang; Georgakopoulou, Aphrodite; Newby, Gregory A.; Everette, Kelcee A.; Nizamis, Evangelos; Paschoudi, Kiriaki; Vlachaki, Efthymia; Gil, Sucheol; Anderson, Anna K.; Koob, Theodore; Huang, Lishan; Wang, Hongjie; Kiem, Hans-Peter; Liu, David R.; Yannaki, Evangelia; Lieber, Andre
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Properties of Adenovirus Vectors with Increased Affinity to DSG2 and the Potential Benefits of Oncolytic Approaches and Gene Therapy
err2022-08-21
err7
errOAAI
errBahlmann, Nora A.; Tsoukas, Raphael L.; Erkens, Sebastian; Wang, Hongjie; Jonsson, Franziska; Aydin, Malik; Naumova, Ella A.; Lieber, Andre; Ehrhardt, Anja; Zhang, Wenli
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In vivo HSC transduction in rhesus macaques with an HDAd5/3+vector targeting desmoglein 2 and transiently overexpressing cxcr4
err2022-07-29
err18
errOAAI
errWang, Hongjie; Germond, Audrey; Li, Chang; Gil, Sucheol; Kim, Jiho; Kiem, Hans-Peter; Lieber, Andre
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Translational development of a tumor junction opening technology
err2022-05-11
err4
errOAAI
errKim, Jiho; Li, Chang; Wang, Hongjie; Kaviraj, Swarnendu; Singh, Sanjay; Savergave, Laxman; Raghuwanshi, Arjun; Gil, Sucheol; Germond, Audrey; Baldessari, Audrey; Chen, Bingmae; Roffler, Steve; Fender, Pascal; Drescher, Charles; Carter, Darrick; Lieber, Andre
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Incomplete Description
err2021-09-06
err0
errOAAI
errLieber, Andre; Scheuermann-Poley, Catharina
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Single-dose MGTA-145/plerixafor leads to efficient mobilization and in vivo transduction of HSCs with thalassemia correction in mice
err2021-03-01
err13
errOAAI
errLi, Chang; Goncalves, Kevin A.; Rasko, Tamas; Pande, Amit; Gil, Sucheol; Liu, Zhinan; Izsvak, Zsuzsanna; Papayannopoulou, Thalia; Davis, John C.; Kiem, Hans-Peter; Lieber, Andre
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In vivo HSPC gene therapy with base editors allows for efficient reactivation of fetal γ-globin in β-YAC mice
err2021-02-23
err62
errOAAI
errLi, Chang; Georgakopoulou, Aphrodite; Mishra, Arpit; Gil, Sucheol; Hawkins, R. David; Yannaki, Evangelia; Lieber, Andre
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In Vivo HSC Gene Therapy Using a Bi-modular HDAd5/35++ Vector Cures Sickle Cell Disease in a Mouse Model
err2021-02-01
err54
errOAAI
errLi, Chang; Wang, Hongjie; Georgakopoulou, Aphrodite; Gil, Sucheol; Yannaki, Evangelia; Lieber, Andre
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Desmoglein-2 as a prognostic and biomarker in ovarian cancer
err2020-11-20
err22
errOAAI
errKim, Jiho; Beidler, Peter; Wang, Hongjie; Li, Chang; Quassab, Abdullah; Coles, Cari; Drescher, Charles; Carter, Darrick; Lieber, Andre
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Binding Mechanism Elucidation of the Acute Respiratory Disease Causing Agent Adenovirus of Serotype 7 to Desmoglein-2
err2020-09-25
err7
errOAAI
errHograindleur, Marc-Andre; Effantin, Gregory; Fenel, Daphna; Mas, Caroline; Lieber, Andre; Schoehn, Guy; Fender, Pascal; Vassal-Stermann, Emilie
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Curative in vivo hematopoietic stem cell gene therapy of murine thalassemia using large regulatory elements
err2020-08-20
err22
errOAAI
errWang, Hongjie; Georgakopoulou, Aphrodite; Li, Chang; Liu, Zhinan; Gil, Sucheol; Bashyam, Ashvin; Yannaki, Evangelia; Anagnostopoulos, Achilles; Pande, Amit; Izsvak, Zsuzsanna; Papayannopoulou, Thalia; Lieber, Andre
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