arrow
M

Michael J. Gait

MRC Laboratory Molecular Biology
H指数:68
被引数:1.4万

个人简介

暂无内容

教育背景

暂无内容

工作经历

暂无内容

荣誉奖项

暂无内容

Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model

穿膜肽偶联的剪接转换寡核苷酸可缓解BTK/Tec双缺陷型X连锁无丙种球蛋白血症模型的表型

2025-01-010
OA
Dystrophin involvement in peripheral circadian SRF signalling
2021-08-134
OAAI
Cmah-dystrophin deficient mdx mice display an accelerated cardiac phenotype that is improved following peptide-PMO exon skipping treatment

Cmah-肌营养不良蛋白缺陷型mdx小鼠表现出加速的心脏表型,在肽-PMO外显子跳跃处理后得到改善

2018-10-0210
OAAI
Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy

系统性肽介导的寡核苷酸治疗可改善脊髓性肌萎缩症的长期生存率

2016-09-12158
OAAI
Self-Assembly into Nanoparticles Is Essential for Receptor Mediated Uptake of Therapeutic Antisense Oligonucleotides
2015-06-1588
OAAI