未登录Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors
Gapinske, Michael; Winter, Jackson; Swami, Devyani; Gapinske, Lauren; Woods, Wendy S.; Shirguppe, Shraddha; Miskalis, Angelo; Busza, Anna; Joulani, Dana; Kao, Collin J.; Kostan, Kurt; Bigot, Anne; Bashir, Rashid; Perez-Pinera, Pablo
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