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Generalizable features of pegRNA design for prime editing of inherited retinal diseases pegRNA设计的通用特征:用于治疗遗传性视网膜疾病的碱基编辑 Patterson, Freya M.; Tran, Minh Thuan Nguyen; Guinan, Thomas; Khalid, Mohd Khairul Nizam Mohd; Kc, Rajendra; Fairfax, Kirsten A.; Liu, Guei-Sheung; Cook, Anthony L.; Hung, Sandy S.; Hewitt, Alex W. 分享 收藏
Magnetic-Guided Delivery of Antisense Oligonucleotides for Targeted Transduction in Multiple Retinal Explant and Organoid Models 磁性引导的 antisense oligonucleotides 递送在多种视网膜外植体和类器官模型中的靶向转导应用 Ye, XH; Chen, SH; Xiong, W; Wang, F; Chan, HF; Lai, HC; Guo, XY; Yang, TT; Shen, SH; Chen, H; Wang, WX; Liu, GS; Guo, YL; Chen, JS 分享 收藏
Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina 视网膜中具有紧凑CRISPR-Cas13的RNA编辑和基因治疗的表征 Kumar, Satheesh; Hsiao, Yi - Wen; Wong, Vickie H. Y.; Aubin, Deborah; Wang, Jiang - Hui; Lisowski, Leszek; Rakoczy, Elizabeth P.; Li, Fan; Martinez, Luis Alarcon -; Cordero, Anai Gonzalez -; Bui, Bang V.; Liu, Guei-Sheung 分享 收藏
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Deep Learning-Based Identification of Intraocular Pressure-Associated Genes Influencing Trabecular Meshwork Cell Morphology Greatbatch, Connor J.; Lu, Qinyi; Hung, Sandy; Tran, Son N.; Wing, Kristof; Liang, Helena; Han, Xikun; Zhou, Tiger; Siggs, Owen M.; Mackey, David A.; Liu, Guei-Sheung; Cook, Anthony L.; Powell, Joseph E.; Craig, Jamie E.; Macgregor, Stuart; Hewitt, Alex W. 分享 收藏
High throughput functional profiling of genes at intraocular pressure loci reveals distinct networks for glaucoma Greatbatch, Connor J.; Lu, Qinyi; Hung, Sandy; Barnett, Alexander J.; Wing, Kristof; Liang, Helena; Han, Xikun; Zhou, Tiger; Siggs, Owen M.; Mackey, David A.; Cook, Anthony L.; Senabouth, Anne; Liu, Guei-Sheung; Craig, Jamie E.; Macgregor, Stuart; Powell, Joseph E.; Hewitt, Alex W. 分享 收藏
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Functional Peptide-Loaded Gelatin Nanoparticles as Eyedrops for Cornea Neovascularization Treatment Chu, Ya-Chun; Fang, Hsu-Wei; Wu, Yu-Yi; Tang, Yu -Jun; Hsieh, Erh-Hsuan; She, YiZhou; Chang, Che-Yi; Lin, I. -Chan; Chen, Yin-Ju; Liu, Guei-Sheung; Tseng, Ching -Li 分享 收藏
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TAK1 blockade as a therapy for retinal neovascularization Wang, Jiang-Hui; Lin, Fan-Li; Chen, Jinying; Zhu, Linxin; Chuang, Yu-Fan; Tu, Leilei; Ma, Chenkai; Ling, Damien; Hewitt, Alex W.; Tseng, Ching-Li; Shah, Manisha H.; Bui, Bang V.; van Wijngaarden, Peter; Dusting, Gregory J.; Wang, Peng-Yuan; Liu, Guei-Sheung 分享 收藏
A novel small molecule inhibitor of human Drp1 Rosdah, Ayeshah A.; Abbott, Belinda M.; Langendorf, Christopher G.; Deng, Yali; Truong, Jia Q.; Waddell, Helen M. M.; Ling, Naomi X. Y.; Smiles, William J.; Delbridge, Lea M. D.; Liu, Guei-Sheung; Oakhill, Jonathan S.; Lim, Shiang Y.; Holien, Jessica K. 分享 收藏
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An Integrative Multi-Omics Analysis Reveals MicroRNA-143 as Potential Therapeutics to Attenuate Retinal Angiogenesis Wang, Jiang-Hui; Chuang, Yu-Fan; Chen, Jinying; Singh, Vikrant; Lin, Fan-Li; Wilson, Richard; Tu, Leilei; Ma, Chenkai; Wong, Raymond C. B.; Wang, Peng-Yuan; Zhong, Jingxiang; Hewitt, Alex W.; van Wijngaarden, Peter; Dusting, Gregory J.; Liu, Guei-Sheung 分享 收藏
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