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Scot A. Wolfe

University of Massachusetts

60H指数
179论文数
1.4W被引数
收录论文 76
发表时间
Prime assembly with linear DNA donors enables large genomic insertions线性DNA供体介导的质粒组装实现大规模基因组插入
errNature
IF48.5
err2026-04-29
err0
PREAI
errBin Liu; Andrew Petti; Xuntao Zhou; Haoyang Cheng; Jenny Gao; Matthew Yee; Youwei Qiao; Yanjun Zhang; Lin Zhou; Scot A. Wolfe; Tingting Jiang; Erik J. Sontheimer; Wen Xue
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Adissp activates insulin-independent glucose disposal and energy expenditure in white fat to treat diabetes and cardiometabolic diseaseAdissp 通过激活白色脂肪中胰岛素非依赖性葡萄糖利用和能量消耗来治疗糖尿病和心血管代谢疾病
err2026-04-24
err0
errOAAI
errLei Huang; Pengpeng Liu; Qingbo Chen; Kai Hu; Shaoxian Li; Alexandra Lee; Martin Wabitsch; Lihua Julie Zhu; Qing Yu; Roger Davis; Michael P. Czech; Scot A. Wolfe; Yong-Xu Wang
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Modular Platform for Therapeutic Drug Delivery Using Trifunctional Bio-Orthogonal Macromolecular Conjugates基于三功能生物正交大分子偶联物的治疗药物递送模块化平台
err2025-11-10
err0
PREAI
errDanmeng Luo; Ning Wang; Hannah Major-Monfried; John Ralls; Sophia Rha; Stacy A. Maitland; Karthikeyan Ponnienselvan; Makiko Yamada; Daniel E. Bauer; Scot A. Wolfe; Alex Kentsis
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Direct delivery of Cas-embedded cytosine base editors as ribonucleoprotein complexes for efficient and accurate editing of clinically relevant targets
err2024-12-16
err0
errOAAI
errLee, Jeong Min; Zeng, Jing; Liu, Pengpeng; Nguyen, My Anh; Loustaunau, Diego Suchenski; Bauer, Daniel E.; Yilmaz, Nese Kurt; Wolfe, Scot A.; Schiffer, Celia A.
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The co-receptor Neuropilin-1 enhances proliferation in inv(16) acute myeloid leukemia via VEGF signaling
errLEUKEMIA
IF13.4
err2024-11-21
err0
PREAI
errHegde, Mahesh; Ahmad, Mohd H.; Lazaro, Roger Mulet; Sugita, Mayumi; Li, Rui; Hu, Kai; Gebhard, Claudia; Guzman, Monica L.; Bushweller, John H.; Zhu, Lihua J.; Brehm, Michael; Wolfe, Scot A.; Delwel, Ruud; Castilla, Lucio H.
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Increasing intracellular dNTP levels improves prime editing efficiency
err2024-09-25
err1
PREAI
errLiu, Pengpeng; Ponnienselvan, Karthikeyan; Nyalile, Thomas; Oikemus, Sarah; Joynt, Anya T.; Iyer, Sukanya; Kelly, Karen; Guo, Dongsheng; Kyawe, Pyae P.; Vanderleeden, Emma; Redick, Sambra D.; Huang, Lei; Chen, Zexiang; Lee, Jeong Min; Schiffer, Celia A.; Harlan, David M.; Wang, Jennifer P.; Emerson Jr, Charles P.; Lawson, Nathan D.; Watts, Jonathan K.; Sontheimer, Erik J.; Luban, Jeremy; Wolfe, Scot A.
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Runx1-R188Q germ line mutation induces inflammation and predisposition to hematologic malignancies in mice
err2023-12-01
err2
errOAAI
errAhmad, Mohd Hafiz; Hegde, Mahesh; Wong, Waihay J.; Mohammadhosseini, Mona; Garrett, Lisa; Carrascoso, Anneliese; Issac, Neethu; Ebert, Benjamin; Silva, Jeffrey C.; Pihan, German; Zhu, Lihua J.; Wolfe, Scot A.; Agarwal, Anupriya; Liu, P. Paul; Castilla, Lucio H.
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Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo
err2023-11-30
err5
errOAAI
errZhang, Han; Kelly, Karen; Lee, Jonathan; Echeverria, Dimas; Cooper, David; Panwala, Rebecca; Amrani, Nadia; Chen, Zexiang; Gaston, Nicholas; Wagh, Atish; Newby, Gregory A.; Xie, Jun; Liu, David R.; Gao, Guangping; Wolfe, Scot A.; Khvorova, Anastasia; Watts, Jonathan K.; Sontheimer, Erik J.
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Generation and application of endogenously floxed alleles for cell-specific knockout in zebrafish
err2023-11-01
err3
errOAAI
errShin, Masahiro; Yin, Hui-Min; Shih, Yu-Huan; Nozaki, Takayuki; Portman, Daneal; Toles, Benjamin; Kolb, Amy; Luk, Kevin; Isogai, Sumio; Ishida, Kinji; Hanasaka, Tomohito; Parsons, Michael J.; Wolfe, Scot A.; Burns, Caroline E.; Burns, C. Geoffrey; Lawson, Nathan D.
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Crosstalk between corepressor NRIP1 and cAMP signaling on adipocyte thermogenic programming
err2023-10-01
err2
errOAAI
errTsagkaraki, Emmanouela; Guilherme, Adilson; Nicoloro, Sarah M.; Kelly, Mark; Lifshitz, Lawrence M.; Wang, Hui; Min, Kyounghee; Rowland, Leslie A.; Santos, Kaltinaitis B.; Wetoska, Nicole; Friedline, Randall H.; Maitland, Stacy A.; Chen, Min; Weinstein, Lee S.; Wolfe, Scot A.; Kim, Jason K.; Czech, Michael P.
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Transcriptional and chromatin profiling of human blood innate lymphoid cell subsets sheds light on HIV-1 pathogenesis
err2023-06-29
err2
errOAAI
errWang, Yetao; Lifshitz, Lawrence; Silverstein, Noah J.; Mintzer, Esther; Luk, Kevin; StLouis, Pamela; Brehm, Michael A.; Wolfe, Scot A.; Deeks, Steven G.; Luban, Jeremy
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Reducing the inherent auto-inhibitory interaction within the pegRNA enhances prime editing efficiency
err2023-05-29
err19
errOAAI
errPonnienselvan, Karthikeyan; Liu, Pengpeng; Nyalile, Thomas; Oikemus, Sarah; Maitland, Stacy A.; Lawson, Nathan D.; Luban, Jeremy; Wolfe, Scot A.
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Genome-wide profiling of prime editor off-target sites in vitro and in vivo using PE-tag使用pe-tag在体外和体内对prime editor脱靶位点进行全基因组分析
err2023-05-08
err22
PREAI
errLiang, Shun-Qing; Liu, Pengpeng; Ponnienselvan, Karthikeyan; Suresh, Sneha; Chen, Zexiang; Kramme, Christian; Chatterjee, Pranam; Zhu, Lihua Julie; Sontheimer, Erik J.; Xue, Wen; Wolfe, Scot A.
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From mouse to sheep: Generating a sheep model and developing a gene therapy for sialidosis
err2023-02-01
err0
PREAI
errGallagher, Jillian; Gallant, Judith; Xu, Ping; Gately, Rachael; Bertrand, Stephanie; McElroy, Abigail; Hall, Erin; Benatti, Hector; Prestigiacomo, Rachel; Luk, Kevin; Fremuth, Leigh E.; van de Vlekkert, Diantha; Hu, Huimin; Toro, Camilo; d'Azzo, Alessandra; Tifft, Cynthia J.; Wolfe, Scot; Rivera, Jaime; Sena-Esteves, Miguel; Gray-Edwards, Heather
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Human genetic diversity alters off-target outcomes of therapeutic gene editing人类遗传多样性改变治疗性基因编辑的脱靶结果
err2022-12-15
err46
errOAAI
errCancellieri, Samuele; Zeng, Jing; Lin, Linda Yingqi; Tognon, Manuel; Nguyen, My Anh; Lin, Jiecong; Bombieri, Nicola; Maitland, Stacy A.; Ciuculescu, Marioara-Felicia; Katta, Varun; Tsai, Shengdar Q.; Armant, Myriam; Wolfe, Scot A.; Giugno, Rosalba; Bauer, Daniel E.; Pinello, Luca
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Efficient Homology-Directed Repair with Circular Single-Stranded DNA Donors环状单链DNA供体的高效同源定向修复
err2022-10-01
err19
errOAAI
errIyer, Sukanya; Mir, Aamir; Vega-Badillo, Joel; Roscoe, Benjamin P.; Ibraheim, Raed; Zhu, Lihua Julie; Lee, Jooyoung; Liu, Pengpeng; Luk, Kevin; Mintzer, Esther; Guo, Dongsheng; Soares de Brito, Josias; Emerson Jr, Charles P.; Zamore, Phillip D.; Sontheimer, Erik J.; Wolfe, Scot A.
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A flexible split prime editor using truncated reverse transcriptase improves dual-AAV delivery in mouse liver
err2022-03-01
err73
errOAAI
errZheng, Chunwei; Liang, Shun-Qing; Liu, Bin; Liu, Pengpeng; Kwan, Suet-Yan; Wolfe, Scot A.; Xue, Wen
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LONP-1 and ATFS-1 sustain deleterious heteroplasmy by promoting mtDNA replication in dysfunctional mitochondria
err2022-02-14
err46
errOAAI
errYang, Qiyuan; Liu, Pengpeng; Anderson, Nadine S.; Shpilka, Tomer; Du, YunGuang; Naresh, Nandhitha Uma; Li, Rui; Zhu, Lihua Julie; Luk, Kevin; Lavelle, Josh; Zeinert, Rilee D.; Chien, Peter; Wolfe, Scot A.; Haynes, Cole M.
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Sialidosis: From gene editing to gene therapy
err2022-02-01
err0
PREAI
errGallagher, Jillian; Gallant, Judith; Xu, Ping; Gately, Rachael; Bertrand, Stephanie; Luk, Kevin; Toro, Camilo; d'Azzo, Alessandra; Wolfe, Scot; Rivera, Jaime; Sena-Esteves, Miguel; Gray-Edwards, Heather
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Genome-wide detection of CRISPR editing in vivo using GUIDE-tag
err2022-01-21
err27
errOAAI
errLiang, Shun-Qing; Liu, Pengpeng; Smith, Jordan L.; Mintzer, Esther; Maitland, Stacy; Dong, Xiaolong; Yang, Qiyuan; Lee, Jonathan; Haynes, Cole M.; Zhu, Lihua Julie; Watts, Jonathan K.; Sontheimer, Erik J.; Wolfe, Scot A.; Xue, Wen
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