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Pridopidine treatment in ALS: subgroup analyses from the HEALEY ALS Platform trial 普利多匹定治疗ALS: 来自HEALEY ALS平台试验的亚组分析 Geva, Michal; Goldberg, Y. Paul; Leitner, Melanie L.; Cruz-Herranz, Andres; Hand, Randal; Chen, Kelly; Gershoni Emek, Noga; Tan, Andrew M.; Paganoni, Sabrina; Berry, James D.; Macklin, Eric A.; Shefner, Jeremy M.; Cudkowicz, Merit E.; Hayden, Michael R. 分享 收藏
Design considerations for C9orf72 disease prevention trials C9orf72疾病预防试验的设计考虑 Benatar, Michael; Staffaroni, Adam M.; Wuu, Joanne; McDermott, Michael P.; Quintana, Melanie; Swidler, Jean; Andersen, Gail; Huey, Edward D.; Turner, Martin R.; Macklin, Eric A.; Berry, James D.; McMillan, Corey T.; Gendron, Tania; Onyike, Chiadi; Rosen, Howard; Heuer, Hilary W.; Grignon, Anne-Laure; Dave, Kuldip D.; Balas, Calaneet; Gleixner, Amanda; Satlin, Andrew; Dunn, Billy; Dacks, Penny; Boxer, Adam L. 分享 收藏
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Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis, A Randomized Clinical Trial Zilucoplan治疗肌萎缩侧索硬化症的疗效与安全性:一项随机临床试验 Paganoni, Sabrina; Fournier, Christina N.; Macklin, Eric A.; Chibnik, Lori B.; Quintana, Melanie; Saville, Benjamin R.; Detry, Michelle A.; Vestrucci, Matteo; Marion, Joe; Mcglothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A.; Yu, Hong; Sherman, Alexander V.; Shefner, Jeremy M.; Hall, Meghan; Kittle, Gale; Berry, James D.; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H.; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J.; Simmons, Zachary; Miller, Timothy M.; Olney, Nicholas; Weiss, Michael D.; Goutman, Stephen A.; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A.; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S.; Arcila-Londono, Ximena; Jackson, Carlayne E.; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B.; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Kasarskis, Edward J.; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; Mcilduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A.; Cohen, Jeffrey A.; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R.; Wymer, James P.; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L.; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W.; Cudkowicz, Merit E. 分享 收藏
Prognostic clinical and biological markers for amyotrophic lateral sclerosis disease progression: validation and implications for clinical trial design and analysis Benatar, Michael; Macklin, Eric A.; Malaspina, Andrea; Rogers, Mary-Louise; Hornstein, Eran; Lombardi, Vittoria; Renfrey, Danielle; Shepheard, Stephanie; Magen, Iddo; Cohen, Yahel; Granit, Volkan; Statland, Jeffrey M.; Heckmann, Jeannine M.; Rademakers, Rosa; McHutchison, Caroline A.; Petrucelli, Leonard; McMillan, Corey T.; Wuu, Joanne 分享 收藏
Apilimod dimesylate in C9orf72 amyotrophic lateral sclerosis: a randomized phase 2a clinical trial Babu, Suma; Nicholson, Katharine A.; Rothstein, Jeffrey D.; Swenson, Andrea; Sampognaro, Paul J.; Pant, Pravin; Macklin, Eric A.; Spruill, Susan; Paganoni, Sabrina; Gendron, Tania F.; Prudencio, Mercedes; Petrucelli, Leonard; Nix, Darrell; Landrette, Sean; Nkrumah, Esther; Fandrick, Keith; Edwards, Joan; Young, Peter R. 分享 收藏
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Addressing the Chronic Pain-Early Cognitive Decline Comorbidity Among Older Adults: Protocol for the Active Brains Remote Efficacy Trial Vranceanu, Ana-Maria; Choukas, Nathaniel R.; Rochon, Elizabeth A.; Duarte, Brooke; Pietrzykowski, Malvina O.; McDermott, Katherine; Hooker, Julia E.; Kulich, Ronald; Quiroz, Yakeel T.; Parker, Robert A.; Macklin, Eric A.; Ritchie, Christine; Mace, Ryan A. 分享 收藏
Safety, tolerability, and preliminary efficacy of SYN120, a dual 5-HT6/5-HT2A antagonist, for the treatment of Parkinson disease dementia: A randomized, controlled, proof-of-concept trial Fernandez, Hubert H.; Weintraub, Daniel; Macklin, Eric; Litvan, Irene; Schwarzschild, Michael A.; Eberling, Jamie; Videnovic, Aleksandar; Kenney, Christopher J. 分享 收藏
Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis Quintana, Melanie R.; Saville, Benjamin; Vestrucci, Matteo A.; Detry, Michelle; Chibnik, Lori; Shefner, Jeremy D.; Berry, James; Chase, Marianne; Andrews, Jinsy V.; Sherman, Alexander; Yu, Hong; Drake, Kristin; Cudkowicz, Merit; Paganoni, Sabrina A.; Macklin, Eric; HEALEY ALS Platform Trial Study Grp 分享 收藏
Evidence for Survival Benefit in ALS with CNM-Au8 Treatment Across Three Study Populations Berry, James; Maragakis, Nicholas; Paganoni, Sabrina; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Detry, Michelle; Menon, Parvathi; Huynh, William; Mahoney, Colin; Stommel, Elijah; Hall, Meghan; Connolly, Mariah; Kittle, Gale; Chase, Marianne; Sherman, Alexander; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; Glanzman, Robert; Hotchkin, Michael; Vucic, Steve; Kiernan, Matthew; Cudkowicz, Merit 分享 收藏
Results from the first four regimens of the HEALEY ALS Platform Trial Paganoni, Sabrina; Berry, James; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Fournier, Christina; Babu, Suma; Maragakis, Nicholas; Oskarsson, Bjorn; Detry, Michelle; Chase, Marianne; Sherman, Alex; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; McGlothlin, Anna; Marion, Joseph; Duda, Petra; Harvey, Brittany; Qureshi, Irfan; Donohue, Mary; Granit, Volkan; Grossman, Katheryn; Glanzman, Robert; Hotchkin, Michael; Goldberg, Y. Paul; Leitner, Melanie; Hayden, Michael; Cudkowicz, Merit 分享 收藏
Metabolomic Profiling of Plasma Samples from PPMI Identifies Molecular Signatures of Parkinson's Disease and Genetic Parkinson's Disease Susceptibility Huntwork-Rodriguez, Sarah; Suh, Jung; Crotty, Grace; Maciuca, Romeo; Macklin, Eric; Davis, Sonnet; Alkabsh, Jamal; Bakshi, Rachit; Chen, Xiqun; Molsberry, Samantha; Ascherio, Alberto; Schwarzschild, Michael 分享 收藏
Enrollment of Participants From Marginalized Racial and Ethnic Groups A Comparative Assessment of the STEADY-PD III and SURE-PD3 Trials Di Luca, Daniel G.; Macklin, Eric A.; Hodgeman, Karen; Lopez, Gisel; Pothier, Lindsay; Callahan, Katherine F.; Lowell, Jill; Chan, James; Videnovic, Aleksandar; Lungu, Codrin; Lang, Anthony E.; Litvan, Irene; Schwarzschild, Michael A.; Simuni, Tatyana 分享 收藏