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A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies Wilk, Jordan; Aggarwal, Varun; Pauley, Mike; Corey, Diane; Conrado, Daniela J.; Lingineni, Karthik; Morales, Juan Francisco; Yoon, Deok Yong; Zhang, Yi; Cui, Zihan; Burton, Jackson; Larkindale, Jane; Ma, Shu Chin; Hovinga, Collin; Martinez, Terina; Romero, Klaus; Belfiore-Oshan, Ramona; Kim, Sarah 分享 收藏
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Type 1 diabetes prevention clinical trial simulator: Case reports of model-informed drug development tool Morales, Juan Francisco; Klose, Marian; Hoffert, Yannick; Podichetty, Jagdeep T.; Burton, Jackson; Schmidt, Stephan; Romero, Klaus; O'Doherty, Inish; Martin, Frank; Campbell-Thompson, Martha; Haller, Michael J.; Atkinson, Mark A.; Kim, Sarah 分享 收藏
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Transforming Drug Development for Neurological Disorders: Proceedings from a Multidisease Area Workshop (vol 20, pg 1682 ,2023) Stephenson, Diane; Belfiore-Oshan, Ramona; Karten, Yashmin; Keavney, Jessi; Kwok, D. Kevin; Martinez, Terina; Montminy, Joe; Muller, Martijn L. T. M.; Romero, Klaus; Sivakumaran, Sudhir 分享 收藏
Transforming Drug Development for Neurological Disorders: Proceedings from a Multidisease Area Workshop Stephenson, Diane; Belfiore-Oshan, Ramona; Karten, Yashmin; Keavney, Jessi; Kwok, D. Kevin; Martinez, Terina; Montminy, Joe; Muller, Martijn L. T. M.; Romero, Klaus; Sivakumaran, Sudhir 分享 收藏
Longitudinal estimated glomerular filtration rate (eGFR) modeling in long-term renal function to inform clinical trial design in kidney transplantation Kosinski, Luke; Frey, Eric; Klein, Amanda; O'Doherty, Inish; Romero, Klaus; Stegall, Mark; Helantera, Ilkka; Gaber, Ahmed Osama E.; Fitzsimmons, William; Aggarwal, Varun 分享 收藏
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Disease progression joint model predicts time to type 1 diabetes onset: Optimizing future type 1 diabetes prevention studies Morales, Juan Francisco; Muse, Rhoda; Podichetty, Jagdeep T.; Burton, Jackson; David, Sarah; Lang, Patrick; Schmidt, Stephan; Romero, Klaus; O'Doherty, Inish; Martin, Frank; Campbell-Thompson, Martha; Haller, Michael J.; Atkinson, Mark A.; Kim, Sarah 分享 收藏
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Recommendations to address key recruitment challenges of Alzheimer's disease clinical trials 解决阿尔茨海默病临床试验关键招募挑战的建议 Langbaum, Jessica B.; Zissimopoulos, Julie; Au, Rhoda; Bose, Niranjan; Edgar, Chris J.; Ehrenberg, Evan; Fillit, Howard; Hill, Carl, V; Hughes, Lynne; Irizarry, Michael; Kremen, Sarah; Lakdawalla, Darius; Lynn, Nancy; Malzbender, Kristina; Maruyama, Tetsuyuki; Massett, Holly A.; Patel, Deep; Peneva, Desi; Reiman, Eric M.; Romero, Klaus; Routledge, Carol; Weiner, Michael W.; Weninger, Stacie; Aisen, Paul S. 分享 收藏
Sputum lipoarabinomannan (LAM) as a biomarker to determine sputum mycobacterial load: exploratory and model-based analyses of integrated data from four cohorts Jones, Aksana; Saini, Jay; Kriel, Belinda; Via, Laura E.; Cai, Yin; Allies, Devon; Hanna, Debra; Hermann, David; Loxton, Andre G.; Walzl, Gerhard; Diacon, Andreas H.; Romero, Klaus; Higashiyama, Ryo; Liu, Yongge; Berg, Alexander 分享 收藏
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Development of a model-based clinical trial simulation platform to optimize the design of clinical trials for Duchenne muscular dystrophy Lingineni, Karthik; Aggarwal, Varun; Morales, Juan Francisco; Conrado, Daniela J.; Corey, Diane; Vong, Camille; Burton, Jackson; Larkindale, Jane; Romero, Klaus; Schmidt, Stephan; Kim, Sarah 分享 收藏
Development of physiologically-based pharmacokinetic models for standard of care and newer tuberculosis drugs 开发用于护理标准和新型结核病药物的基于生理的药代动力学模型 Humphries, Helen; Almond, Lisa; Berg, Alexander; Gardner, Iain; Hatley, Oliver; Pan, Xian; Small, Ben; Zhang, Mian; Jamei, Masoud; Romero, Klaus 分享 收藏
DEVELOPMENT OF THE HUNTINGTON'S DISEASE INTEGRATED STAGING SYSTEM (HD-ISS) Tabrizi, Sarah; Schobel, Scott; Gantman, Emily; Mansbach, Alexandra; Borowsky, Beth; Konstantinova, Pavlina; Mestre, Tiago; Mullin, Ariana; Panagoulias, Jennifer; Romero, Klaus; Ross, Christopher A.; Sivakumaran, Sudhir; Turner, Emily; Zauderer, Maurice; Long, Jeff; Sampaio, Cristina 分享 收藏
A Disease Progression Model to Quantify the Nonmotor Symptoms of Parkinson's Disease in Participants With Leucine-Rich Repeat Kinase 2 Mutation Ahamadi, Malidi; Mehrotra, Nitin; Hanan, Nathan; Lai Yee, Ka; Gheyas, Ferdous; Anton, Judith; Bani, Massimo; Boroojerdi, Babak; Smit, Hans; Weidemann, Jonas; Macha, Sreeraj; Thuillier, Vincent; Chen, Chao; Yang, Minhua; Williams-Gray, Caroline H.; Stebbins, Glenn T.; Pagano, Gennaro; Hang, Yaming; Marek, Kenneth; Venuto, Charles S.; Javidnia, Monica; Dexter, David; Pedata, Anne; Stafford, Bob; Akalu, Mussie; Stephenson, Diane; Romero, Klaus; Sinha, Vikram 分享 收藏