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Altered muscle niche contributes to myogenic deficit in the D2-mdx model of severe DMD Mazala, Davi A. G.; Hindupur, Ravi; Moon, Young Jae; Shaikh, Fatima; Gamu, Iteoluwakishi H.; Alladi, Dhruv; Panci, Georgiana; Weiss-Gayet, Michele; Chazaud, Benedicte; Partridge, Terence A.; Novak, James S.; Jaiswal, Jyoti K. 分享 收藏
Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy Klimek, Margaret E. Benny; Vila, Maria Candida; Edwards, Katie; Boehler, Jessica; Novak, James; Zhang, Aiping; Van der Meulen, Jack; Tatum, Kathleen; Quinn, James; Fiorillo, Alyson; Burki, Umar; Straub, Volker; Lu, Qi Long; Hathout, Yetrib; van Den Anker, John; Partridge, Terence A.; Morales, Melissa; Hoffman, Eric; Nagaraju, Kanneboyina 分享 收藏
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Interrogation of Dystrophin and Dystroglycan Complex Protein Turnover After Exon Skipping Therapy Novak, James S.; Spathis, Rita; Dang, Utkarsh J.; Fiorillo, Alyson A.; Hindupur, Ravi; Tully, Christopher B.; Mazala, Davi A. G.; Canessa, Emily; Brown, Kristy J.; Partridgea, Terence A.; Hathout, Yetrib; Nagaraju, Kanneboyina 分享 收藏
Human muscle stem cells are refractory to aging Novak, James S.; Mazala, Davi A. G.; Nearing, Marie; Hindupur, Ravi; Uapinyoying, Prech; Habib, Nayab F.; Dickson, Tessa; Ioffe, Olga B.; Harris, Brent T.; Fidelia-Lambert, Marie N.; Rossi, Christopher T.; Hill, D. Ashely; Wagner, Kathryn R.; Hoffman, Eric P.; Partridge, Terence A. 分享 收藏
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TGF-β-driven muscle degeneration and failed regeneration underlie disease onset in a DMD mouse model Mazala, Davi A. G.; Novak, James S.; Hogarth, Marshall W.; Nearing, Marie; Adusumalli, Prabhat; Tully, Christopher B.; Habib, Nayab F.; Gordish-Dressman, Heather; Chen, Yi-Wen; Jaiswal, Jyoti K.; Partridge, Terence A. 分享 收藏
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Morpholino-induced exon skipping stimulates cell-mediated and humoral responses to dystrophin in mdx mice Vila, Maria C.; Novak, James S.; Klimek, Margaret Benny; Li, Ning; Morales, Melissa; Fritz, Alexander G.; Edwards, Katie; Boehler, Jessica F.; Hogarth, Marshall W.; Kinder, Travis B.; Zhang, Aiping; Mazala, Davi; Fiorillo, Alyson A.; Douglas, Bonnie; Chen, Yi-Wen; van den Anker, John; Lu, Qi L.; Hathout, Yetrib; Hoffman, Eric P.; Partridge, Terence A.; Nagaraju, Kanneboyina 分享 收藏
Efficacy of Multi-exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates Lim, Kenji Rowel Q.; Echigoya, Yusuke; Nagata, Tetsuya; Kuraoka, Mutsuki; Kobayashi, Masanori; Aoki, Yoshitsugu; Partridge, Terence; Maruyama, Rika; Takeda, Shin'ichi; Yokota, Toshifumi 分享 收藏
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Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle (vol 8, 2017) Novak, James S.; Hogarth, Marshall W.; Boehler, Jessica F.; Nearing, Marie; Vila, Maria C.; Heredia, Raul; Fiorillo, Alyson A.; Zhang, Aiping; Hathout, Yetrib; Hoffman, Eric P.; Jaiswal, Jyoti K.; Nagaraju, Kanneboyina; Cirak, Sebahattin; Partridge, Terence A. 分享 收藏
Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle (vol 8, 941, 2017) Novak, James S.; Hogarth, Marshall W.; Boehler, Jessica F.; Nearing, Marie; Vila, Maria C.; Heredia, Raul; Fiorillo, Alyson A.; Zhang, Aiping; Hathout, Yetrib; Hoffman, Eric P.; Jaiswal, Jyoti K.; Nagaraju, Kanneboyina; Cirak, Sebahattin; Partridge, Terence A. 分享 收藏
Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle Novak, James S.; Hogarth, Marshall W.; Boehler, Jessica F.; Nearing, Marie; Vila, Maria C.; Heredia, Raul; Fiorillo, Alyson A.; Zhang, Aiping; Hathout, Yetrib; Hoffman, Eric P.; Jaiswal, Jyoti K.; Nagaraju, Kanneboyina; Cirak, Sebahattin; Partridge, Terence A. 分享 收藏
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Effect of genetic background on the dystrophic phenotype in mdx mice Coley, William D.; Bogdanik, Laurent; Vila, Maria Candida; Yu, Qing; Van der Meulen, Jack H.; Rayavarapu, Sree; Novak, James S.; Nearing, Marie; Quinn, James L.; Saunders, Allison; Dolan, Connor; Andrews, Whitney; Lammert, Catherine; Austin, Andrew; Partridge, Terence A.; Cox, Gregory A.; Lutz, Cathleen; Nagaraju, Kanneboyina 分享 收藏
TNF-α-Induced microRNAs Control Dystrophin Expression in Becker Muscular Dystrophy Fiorillo, Alyson A.; Heier, Christopher R.; Novak, James S.; Tully, Christopher B.; Brown, Kristy J.; Uaesoontrachoon, Kitipong; Vila, Maria C.; Ngheim, Peter P.; Bello, Luca; Kornegay, Joe N.; Angelini, Corrado; Partridge, Terence A.; Nagaraju, Kanneboyina; Hoffman, Eric P. 分享 收藏