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The co-receptor Neuropilin-1 enhances proliferation in inv(16) acute myeloid leukemia via VEGF signaling Hegde, Mahesh; Ahmad, Mohd H.; Lazaro, Roger Mulet; Sugita, Mayumi; Li, Rui; Hu, Kai; Gebhard, Claudia; Guzman, Monica L.; Bushweller, John H.; Zhu, Lihua J.; Brehm, Michael; Wolfe, Scot A.; Delwel, Ruud; Castilla, Lucio H. Share Save
Increasing intracellular dNTP levels improves prime editing efficiency Liu, Pengpeng; Ponnienselvan, Karthikeyan; Nyalile, Thomas; Oikemus, Sarah; Joynt, Anya T.; Iyer, Sukanya; Kelly, Karen; Guo, Dongsheng; Kyawe, Pyae P.; Vanderleeden, Emma; Redick, Sambra D.; Huang, Lei; Chen, Zexiang; Lee, Jeong Min; Schiffer, Celia A.; Harlan, David M.; Wang, Jennifer P.; Emerson Jr, Charles P.; Lawson, Nathan D.; Watts, Jonathan K.; Sontheimer, Erik J.; Luban, Jeremy; Wolfe, Scot A. Share Save
Runx1-R188Q germ line mutation induces inflammation and predisposition to hematologic malignancies in mice Ahmad, Mohd Hafiz; Hegde, Mahesh; Wong, Waihay J.; Mohammadhosseini, Mona; Garrett, Lisa; Carrascoso, Anneliese; Issac, Neethu; Ebert, Benjamin; Silva, Jeffrey C.; Pihan, German; Zhu, Lihua J.; Wolfe, Scot A.; Agarwal, Anupriya; Liu, P. Paul; Castilla, Lucio H. Share Save
Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo Zhang, Han; Kelly, Karen; Lee, Jonathan; Echeverria, Dimas; Cooper, David; Panwala, Rebecca; Amrani, Nadia; Chen, Zexiang; Gaston, Nicholas; Wagh, Atish; Newby, Gregory A.; Xie, Jun; Liu, David R.; Gao, Guangping; Wolfe, Scot A.; Khvorova, Anastasia; Watts, Jonathan K.; Sontheimer, Erik J. Share Save
Generation and application of endogenously floxed alleles for cell-specific knockout in zebrafish Shin, Masahiro; Yin, Hui-Min; Shih, Yu-Huan; Nozaki, Takayuki; Portman, Daneal; Toles, Benjamin; Kolb, Amy; Luk, Kevin; Isogai, Sumio; Ishida, Kinji; Hanasaka, Tomohito; Parsons, Michael J.; Wolfe, Scot A.; Burns, Caroline E.; Burns, C. Geoffrey; Lawson, Nathan D. Share Save
Crosstalk between corepressor NRIP1 and cAMP signaling on adipocyte thermogenic programming Tsagkaraki, Emmanouela; Guilherme, Adilson; Nicoloro, Sarah M.; Kelly, Mark; Lifshitz, Lawrence M.; Wang, Hui; Min, Kyounghee; Rowland, Leslie A.; Santos, Kaltinaitis B.; Wetoska, Nicole; Friedline, Randall H.; Maitland, Stacy A.; Chen, Min; Weinstein, Lee S.; Wolfe, Scot A.; Kim, Jason K.; Czech, Michael P. Share Save
Transcriptional and chromatin profiling of human blood innate lymphoid cell subsets sheds light on HIV-1 pathogenesis Wang, Yetao; Lifshitz, Lawrence; Silverstein, Noah J.; Mintzer, Esther; Luk, Kevin; StLouis, Pamela; Brehm, Michael A.; Wolfe, Scot A.; Deeks, Steven G.; Luban, Jeremy Share Save
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Genome-wide profiling of prime editor off-target sites in vitro and in vivo using PE-tag Liang, Shun-Qing; Liu, Pengpeng; Ponnienselvan, Karthikeyan; Suresh, Sneha; Chen, Zexiang; Kramme, Christian; Chatterjee, Pranam; Zhu, Lihua Julie; Sontheimer, Erik J.; Xue, Wen; Wolfe, Scot A. Share Save
From mouse to sheep: Generating a sheep model and developing a gene therapy for sialidosis Gallagher, Jillian; Gallant, Judith; Xu, Ping; Gately, Rachael; Bertrand, Stephanie; McElroy, Abigail; Hall, Erin; Benatti, Hector; Prestigiacomo, Rachel; Luk, Kevin; Fremuth, Leigh E.; van de Vlekkert, Diantha; Hu, Huimin; Toro, Camilo; d'Azzo, Alessandra; Tifft, Cynthia J.; Wolfe, Scot; Rivera, Jaime; Sena-Esteves, Miguel; Gray-Edwards, Heather Share Save
Human genetic diversity alters off-target outcomes of therapeutic gene editing Cancellieri, Samuele; Zeng, Jing; Lin, Linda Yingqi; Tognon, Manuel; Nguyen, My Anh; Lin, Jiecong; Bombieri, Nicola; Maitland, Stacy A.; Ciuculescu, Marioara-Felicia; Katta, Varun; Tsai, Shengdar Q.; Armant, Myriam; Wolfe, Scot A.; Giugno, Rosalba; Bauer, Daniel E.; Pinello, Luca Share Save
Efficient Homology-Directed Repair with Circular Single-Stranded DNA Donors Iyer, Sukanya; Mir, Aamir; Vega-Badillo, Joel; Roscoe, Benjamin P.; Ibraheim, Raed; Zhu, Lihua Julie; Lee, Jooyoung; Liu, Pengpeng; Luk, Kevin; Mintzer, Esther; Guo, Dongsheng; Soares de Brito, Josias; Emerson Jr, Charles P.; Zamore, Phillip D.; Sontheimer, Erik J.; Wolfe, Scot A. Share Save
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LONP-1 and ATFS-1 sustain deleterious heteroplasmy by promoting mtDNA replication in dysfunctional mitochondria Yang, Qiyuan; Liu, Pengpeng; Anderson, Nadine S.; Shpilka, Tomer; Du, YunGuang; Naresh, Nandhitha Uma; Li, Rui; Zhu, Lihua Julie; Luk, Kevin; Lavelle, Josh; Zeinert, Rilee D.; Chien, Peter; Wolfe, Scot A.; Haynes, Cole M. Share Save
Sialidosis: From gene editing to gene therapy Gallagher, Jillian; Gallant, Judith; Xu, Ping; Gately, Rachael; Bertrand, Stephanie; Luk, Kevin; Toro, Camilo; d'Azzo, Alessandra; Wolfe, Scot; Rivera, Jaime; Sena-Esteves, Miguel; Gray-Edwards, Heather Share Save
Genome-wide detection of CRISPR editing in vivo using GUIDE-tag Liang, Shun-Qing; Liu, Pengpeng; Smith, Jordan L.; Mintzer, Esther; Maitland, Stacy; Dong, Xiaolong; Yang, Qiyuan; Lee, Jonathan; Haynes, Cole M.; Zhu, Lihua Julie; Watts, Jonathan K.; Sontheimer, Erik J.; Wolfe, Scot A.; Xue, Wen Share Save