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Regulation of MCCC1 expression by a Parkinson's disease-associated intronic variant: implications for pathogenesis Sogabe, Shunsaku; Nakano, Hiroko; Ogasahara, Yusuke; Cha, Pei-Chieng; Ando, Yuko; Taniguchi-Ikeda, Mariko; Matsumoto, Ryusaku; Kanagawa, Motoi; Kobayashi, Kazuhiro; Murayama, Shigeo; Aoi, Takashi; Toda, Tatsushi; Satake, Wataru Share Save
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An investigator-initiated phase II trial of tirabrutinib in patients with relapsed or refractory secondary CNS lymphoma Munakata, W.; Goto, H.; Fukuhara, N.; Nagai, H.; Arima, H.; Kato, K.; Kurishita, K.; Shuda, Y.; Isomura, R.; Ando, Y.; Iwaki, N.; Sadachi, R.; Okita, N.; Izutsu, K. Share Save
TIF1β activates leukemic transcriptional program in HSCs and promotes BCR::ABL1-induced myeloid leukemia Morii, Mariko; Kubota, Sho; Iimori, Mihoko; Yokomizo-Nakano, Takako; Hamashima, Ai; Bai, Jie; Nishimura, Akiho; Tasaki, Masayoshi; Ando, Yukio; Araki, Kimi; Sashida, Goro Share Save
Development of Benziodarone Analogues with Enhanced Potency for Selective Binding to Transthyretin in Human Plasma Mizuguchi, Mineyuki; Nakagawa, Yusuke; Yokoyama, Takeshi; Okada, Takuya; Fujii, Kanako; Takahashi, Kanoko; Luan, Nguyen Ngoc Thanh; Nabeshima, Yuko; Kanamitsu, Kayoko; Nakagawa, Shinsaku; Yamakawa, Shiori; Ueda, Mitsuharu; Ando, Yukio; Toyooka, Naoki Share Save
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Summary Report of a Public Workshop: Case Studies of Multi-Regional Clinical Trial Incorporating Concept of the ICH E17 Guideline Matsushima, Nobuko; Otsubo, Yasuto; Aoi, Yoko; Nakamura, Ryuta; Kaneko, Shuhei; Asakawa, Takashi; Matsuoka, Nobushige; Watabe, Kei; Komiyama, Osamu; Yamamoto, Hideharu; Ando, Yuki Share Save
Characterization of heterozygous ATTR Tyr114Cys amyloidosis-specific induced pluripotent stem cells Ouchi, Kenta; Isono, Kaori; Ohya, Yuki; Shiraki, Nobuaki; Tasaki, Masayoshi; Inomata, Yukihiro; Ueda, Mitsuharu; Era, Takumi; Kume, Shoen; Ando, Yukio; Jono, Hirofumi Share Save
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Myelodysplasia after clonal hematopoiesis with APOBEC3-mediated CYBB inactivation in retroviral gene therapy for X-CGD Uchiyama, Toru; Kawai, Toshinao; Nakabayashi, Kazuhiko; Nakazawa, Yumiko; Goto, Fumihiro; Okamura, Kohji; Nishimura, Toyoki; Kato, Koji; Watanabe, Nobuyuki; Miura, Akane; Yasuda, Toru; Ando, Yukiko; Minegishi, Tomoko; Edasawa, Kaori; Shimura, Marika; Akiba, Yumi; Otsubo, Aiko Sato; Mizukami, Tomoyuki; Kato, Motohir; Akashi, Koichi; Nunoi, Hiroyuki; Onodera, Masafumi Share Save
Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy Coelho, Teresa; Marques, Wilson, Jr.; Dasgupta, Noel R.; Chao, Chi-Chao; Parman, Yesim; Franca, Marcondes Cavalcante, Jr.; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington Share Save
ASO Visual Abstract: Transducin Beta-like 2 is a Potential Driver Gene that Adapts to Endoplasmic Reticulum Stress to Promote Tumor Growth of Lung Adenocarcinoma Kosai, Keisuke; Masuda, Takaaki; Kitagawa, Akihiro; Tobo, Taro; Ono, Yuya; Ando, Yuki; Takahashi, Junichi; Haratake, Naoki; Kohno, Mikihiro; Takenaka, Tomoyoshi; Yoshizumi, Tomoharu; Mimori, Koshi Share Save