未登录 High resistance barrier and prophylactic protection in preclinical models of SARS-CoV-2 with two siRNA combination Anglero-Rodriguez, Yesseinia, I; Lempp, Florian A.; Subramanian, Megha; Mcininch, James; Schlegel, Mark K.; Bohan, Dana; Wong, Emily; Brown, Christopher R.; Foster, Donald J.; Castoreno, Adam B.; Nguyen, Tuyen; Cuffe, Dara; Montiel-Ruiz, Martin; Kaiser, Hannah; Sahakyan, Anna; Spreafico, Roberto; Morskaya, Svetlana Shulga; Barry, Joseph D.; Berman, Daniel; Zhang, Ligang; Lefebvre, Stephanie; Kasper, Anne; Racie, Timothy; Weddle, Diann; Mobley, Melissa; Wassarman, Kelly; Bisbe, Anna; Zlatev, Ivan; Rogers, Arlin; Nechev, Lubomir; Dybowski, Joseph; Chong, Saeho; Nair, Jayaprakash; Simon, Amy; Sloan, Kevin; Hwang, Seungmin; Virgin, Herbert W.; Fitzgerald, Kevin; Maier, Martin A.; Hinkle, Gregory; Hebner, Christy M.; Akinc, Akin; Jadhav, Vasant 分享 收藏
RNAi-mediated rheostat for dynamic control of AAV-delivered transgenes Subramanian, Megha; McIninch, James; Zlatev, Ivan; Schlegel, Mark K.; Kaittanis, Charalambos; Nguyen, Tuyen; Agarwal, Saket; Racie, Timothy; Alvarado, Martha Arbaiza; Wassarman, Kelly; Collins, Thomas S.; Chickering, Tyler; Brown, Christopher R.; Schmidt, Karyn; Castoreno, Adam B.; Shulga-Morskaya, Svetlana; Stamenova, Elena; Buckowing, Kira; Berman, Daniel; Barry, Joseph D.; Bisbe, Anna; Maier, Martin A.; Fitzgerald, Kevin; Jadhav, Vasant 分享 收藏
From bench to bedside: Improving the clinical safety of GalNAc-siRNA conjugates using seed-pairing destabilization Schlegel, Mark K.; Janas, Maja M.; Jiang, Yongfeng; Barry, Joseph D.; Davis, Wendell; Agarwal, Saket; Berman, Daniel; Brown, Christopher R.; Castoreno, Adam; LeBlanc, Sarah; Liebow, Abigail; Mayo, Tara; Milstein, Stuart; Nguyen, Tuyen; Shulga-Morskaya, Svetlana; Hyde, Sarah; Schofield, Sally; Szeto, John; Woods, Lauren Blair; Yilmaz, Vedat O.; Manoharan, Muthiah; Egli, Martin; Charisse, Klaus; Sepp-Lorenzino, Laura; Haslett, Patrick; Fitzgerald, Kevin; Jadhav, Vasant; Maier, Martin A. 分享 收藏
Overcoming GNA/RNA base-pairing limitations using isonucleotides improves the pharmacodynamic activity of ESC plus GalNAc-siRNAs Schlegel, Mark K.; Matsuda, Shigeo; Brown, Christopher R.; Harp, Joel M.; Barry, Joseph D.; Berman, Daniel; Castoreno, Adam; Schofield, Sally; Szeto, John; Manoharan, Muthiah; Charisse, Klaus; Egli, Martin; Maier, Martin A. 分享 收藏
Timer-based proteomic profiling of the ubiquitin-proteasome system reveals a substrate receptor of the GID ubiquitin ligase Kong, Ka-Yiu Edwin; Fischer, Bernd; Meurer, Matthias; Kats, Ilia; Li, Zhaoyan; Ruehle, Frank; Barry, Joseph D.; Kirrmaier, Daniel; Chevyreva, Veronika; San Luis, Bryan-Joseph; Costanzo, Michael; Huber, Wolfgang; Andrews, Brenda J.; Boone, Charles; Knop, Michael; Khmelinskii, Anton 分享 收藏
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Data-analysis strategies for image-based cell profiling 基于图像的细胞轮廓分析的数据分析策略 Caicedo, Juan C.; Cooper, Sam; Heigwer, Florian; Warchal, Scott; Qiu, Peng; Molnar, Csaba; Vasilevich, Aliaksei S.; Barry, Joseph D.; Bansal, Harmanjit Singh; Kraus, Oren; Wawer, Mathias; Paavolainen, Lassi; Herrmann, Markus D.; Rohban, Mohammad; Hung, Jane; Hennig, Holger; Concannon, John; Smith, Ian; Clemons, Paul A.; Singh, Shantanu; Rees, Paul; Horvath, Peter; Linington, Roger G.; Carpenter, Anne E. 分享 收藏
Upregulation of SPS100 gene expression by an antisense RNA via a switch of mRNA isoforms with different stabilities Bunina, Daria; Stefl, Martin; Huber, Florian; Khmelinskii, Anton; Meurer, Matthias; Barry, Joseph D.; Kats, Ilia; Kirrmaier, Daniel; Huber, Wolfgang; Knop, Michael 分享 收藏
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Biggest challenges in bioinformatics Fuller, Jonathan C.; Khoueiry, Pierre; Dinkel, Holger; Forslund, Kristoffer; Stamatakis, Alexandros; Barry, Joseph; Budd, Aidan; Soldatos, Theodoros G.; Linssen, Katja; Rajput, Abdul Mateen 分享 收藏
Tandem fluorescent protein timers for in vivo analysis of protein dynamics Khmelinskii, Anton; Keller, Philipp J.; Bartosik, Anna; Meurer, Matthias; Barry, Joseph D.; Mardin, Balca R.; Kaufmann, Andreas; Trautmann, Susanne; Wachsmuth, Malte; Pereira, Gislene; Huber, Wolfgang; Schiebel, Elmar; Knop, Michael 分享 收藏