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Andrew V. Anzalone

universite de montreal

18H指数
32论文数
1.0W被引数
收录论文 14
发表时间
Prime Editing for p47phox-Deficient Chronic Granulomatous DiseaseGori, J.L.; Haddad, E.; Frangoul, H.; Kohn, D.B.; Morris, E.C.; Martin, B.N.; Deary, B.A.; Nickerson, M.; Scholz, R.L.; Fernandez, I.; et al. 基因组编辑技术用于p47phox缺陷型慢性肉芽肿病。N. Engl. J. Med. 2025. [Google Scholar] [CrossRef] [PubMed]
err2025-12-01
err0
PREAI
errGori, Jennifer L.; Haddad, Elie; Frangoul, Haydar; Kohn, Donald B.; Morris, Emma C.; Martin, Bradley N.; Deary, Briana A.; Nickerson, McKinley; Scholz, Rebecca L.; Fernandez, Isabel; Leveille, Karine; De Ravin, Suk See; Kang, Elizabeth M.; Pierzynski, Marie; Estwick, Tyra; Littel, Patricia; Kuhns, Douglas B.; Long Priel, Debra A.; Teira, Pierre; Turvey, Stuart; Arnold, Jordyn; Evans, Misty D.; McManus, Meghann; Carpenter, Ben; Waterman, David P.; Anzalone, Andrew V.; Petrusich, Alexandria; Osuna, Christa E.; O'Malley, Tiernan T.; Stewart-Ornstein, Jacob; Heath, Jack M.; Nehilla, Barrett J.; Asmal, Mohammed; Malech, Harry L.
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Efficient C•G-to-G•C base editors developed using CRISPRi screens, target-library analysis, and machine learning
err2023-10-18
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errOAAI
errKoblan, Luke W.; Arbab, Mandana; Shen, Max W.; Hussmann, Jeffrey A.; Anzalone, Andrew V.; Doman, Jordan L.; Newby, Gregory A.; Yang, Dian; Mok, Beverly; Replogle, Joseph M.; Xu, Albert; Sisley, Tyler A.; Weissman, Jonathan S.; Adamson, Britt; Liu, David R.
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A prime editor mouse to model a broad spectrum of somatic mutations in vivoprime editor小鼠在体内建立广泛的体细胞突变模型
err2023-05-11
err20
errOAAI
errEly, Zackery A.; Mathey-Andrews, Nicolas; Naranjo, Santiago; Gould, Samuel I.; Mercer, Kim L.; Newby, Gregory A.; Cabana, Christina M.; Rideout III, William M.; Jaramillo, Grissel Cervantes; Khirallah, Jennifer M.; Holland, Katie; Randolph, Peyton B.; Freed-Pastor, William A.; Davis, Jessie R.; Kulstad, Zachary; Westcott, Peter M. K.; Lin, Lin; Anzalone, Andrew V.; Horton, Brendan L.; Pattada, Nimisha B.; Shanahan, Sean-Luc; Ye, Zhongfeng; Spranger, Stefani; Xu, Qiaobing; Sanchez-Rivera, Francisco J.; Liu, David R.; Jacks, Tyler
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Efficient prime editing in mouse brain, liver and heart with dual AAVs
err2023-05-04
err77
errOAAI
errDavis, Jessie R.; Banskota, Samagya; Levy, Jonathan M.; Newby, Gregory A.; Wang, Xiao; Anzalone, Andrew V.; Nelson, Andrew T.; Chen, Peter J.; Hennes, Andrew D.; An, Meirui; Roh, Heejin; Randolph, Peyton B.; Musunuru, Kiran; Liu, David R.
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Programmable deletion, replacement, integration and inversion of large DNA sequences with twin prime editing通过双素数编辑对大DNA序列进行可编程的删除,替换,整合和反转
err2021-12-09
err302
errOAAI
errAnzalone, Andrew, V; Gao, Xin D.; Podracky, Christopher J.; Nelson, Andrew T.; Koblan, Luke W.; Raguram, Aditya; Levy, Jonathan M.; Mercer, Jaron A. M.; Liu, David R.
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Engineered pegRNAs improve prime editing efficiency (vol 40, pg 402, 2022)
err2021-12-08
err2
errOAAI
errNelson, James W.; Randolph, Peyton B.; Shen, Simon P.; Everette, Kelcee A.; Chen, Peter J.; Anzalone, Andrew V.; An, Meirui; Newby, Gregory A.; Chen, Jonathan C.; Hsu, Alvin; Liu, David R.
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Engineered pegRNAs improve prime editing efficiency工程pegRNAs提高了prime编辑效率
err2021-10-04
err394
errOAAI
errNelson, James W.; Randolph, Peyton B.; Shen, Simon P.; Everette, Kelcee A.; Chen, Peter J.; Anzalone, Andrew, V; An, Meirui; Newby, Gregory A.; Chen, Jonathan C.; Hsu, Alvin; Liu, David R.
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Efficient C•G-to-G•C base editors developed using CRISPRi screens, target-library analysis, and machine learning
err2021-06-28
err162
errOAAI
errKoblan, Luke W.; Arbab, Mandana; Shen, Max W.; Hussmann, Jeffrey A.; Anzalone, Andrew V.; Doman, Jordan L.; Newby, Gregory A.; Yang, Dian; Mok, Beverly; Replogle, Joseph M.; Xu, Albert; Sisley, Tyler A.; Weissman, Jonathan S.; Adamson, Britt; Liu, David R.
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PrimeDesign software for rapid and simplified design of prime editing guide RNAsPrimeDesign软件,用于快速和简化设计prime编辑指南rna
err2021-02-15
err115
errOAAI
errHsu, Jonathan Y.; Grunewald, Julian; Szalay, Regan; Shih, Justine; Anzalone, Andrew, V; Lam, Kin Chung; Shen, Max W.; Petri, Karl; Liu, David R.; Joung, J. Keith; Pinello, Luca
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Prime genome editing in rice and wheat
err2020-03-16
err523
PREAI
errLin, Qiupeng; Zong, Yuan; Xue, Chenxiao; Wang, Shengxing; Jin, Shuai; Zhu, Zixu; Wang, Yanpeng; Anzalone, Andrew V.; Raguram, Aditya; Doman, Jordan L.; Liu, David R.; Gao, Caixia
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Reprogramming eukaryotic translation with ligand-responsive synthetic RNA switches
err2016-03-21
err31
errOAAI
errAnzalone, Andrew V.; Lin, Annie J.; Zairis, Sakellarios; Rabadan, Raul; Cornish, Virginia W.
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A Common Diaryl Ether Intermediate for the Gram-Scale Synthesis of Oxazine and Xanthene Fluorophores
err2012-11-21
err45
errOAAI
errAnzalone, Andrew V.; Wang, Tracy Y.; Chen, Zhixing; Cornish, Virginia W.
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Discovery of a Potent Inhibitor of Anaplastic Lymphoma Kinase with in Vivo Antitumor Activity发现具有体内抗肿瘤活性的间变性淋巴瘤激酶的有效抑制剂
err2010-09-01
err48
errOAAI
errOtt, Gregory R.; Tripathy, Rabindranath; Cheng, Mangeng; McHugh, Robert; Anzalone, Andrew V.; Underiner, Ted L.; Curry, Matthew A.; Quail, Matthew R.; Lu, Lihui; Wan, Weihua; Angeles, Thelma S.; Albom, Mark S.; Aimone, Lisa D.; Ator, Mark A.; Ruggeri, Bruce A.; Dorsey, Bruce D.
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