Fontana, Marianna; Berk, John L.; Gillmore, Julian D.; Witteles, Ronald M.; Grogan, Martha; Drachman, Brian; Damy, Thibaud; Garcia-Pavia, Pablo; Taubel, Jorg; Solomon, Scott D.; Sheikh, Farooq H.; Tahara, Nobuhiro; Gonzalez-Costello, Jose; Tsujita, Kenichi; Morbach, Caroline; Pozsonyi, Zoltan; Petrie, Mark C.; Delgado, Diego; van der Meer, Peter; Jabbour, Andrew; Bondue, Antoine; Kim, Darae; Azevedo, Olga; Hvitfeldt Poulsen, Steen; Yilmaz, Ali; Jankowska, Ewa A.; Algalarrondo, Vincent; Slugg, Andrew; Garg, Pushkal P.; Boyle, Katherine L.; Yureneva, Elena; Silliman, Nancy; Yang, Lilli; Chen, Jihong; Eraly, Satish A.; Vest, John; Maurer, Mathew S.

Effects of eplontersen on symptoms of autonomic neuropathy in hereditary transthyretin-mediated amyloidosis: secondary analysis from the NEURO-TTRansform trial

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

IF7.4

2024-11-170

Effect of Eplontersen on Cardiac Structure and Function in Patients With Hereditary Transthyretin Amyloidosis

JOURNAL OF CARDIAC FAILURE

IF8.2

2024-08-015

PRE

Impact of Baseline Neuropathy Severity on Vutrisiran Treatment Response in the Phase 3 HELIOS-A Study

NEUROLOGY AND THERAPY

IF4.8

2024-03-211

OAAI

Impact of vutrisiran on exploratory cardiac parameters in hereditary transthyretin-mediated amyloidosis with polyneuropathy

EUROPEAN JOURNAL OF HEART FAILURE

IF10.8

2024-02-0612

Neurofilament light chain kinetics as a biomarker for polyneuropathy in V122I hereditary transthyretin amyloidosis

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

IF7.4

2023-12-112

PRE

APOLLO-B, a Study of Patisiran in Patients With Transthyretin Cardiac Amyloidosis: Primary LongTerm Results From the Open-Label Extension Period

CIRCULATION

IF38.6

2023-11-070

PRE

Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2023-10-2685

Maurer, Mathew S.; Kale, Parag; Fontana, Marianna; Berk, John L.; Grogan, Martha; Gustafsson, Finn; Hung, Rebecca R.; Gottlieb, Robert L.; Damy, Thibaud; Gonzalez-Duarte, Alejandra; Sarswat, Nitasha; Sekijima, Yoshiki; Tahara, Nobuhiro; Taylor, Mark S.; Kubanek, Milos; Donal, Erwan; Palecek, Tomas; Tsujita, Kenichi; Tang, W. H. Wilson; Yu, Wen-Chung; Obici, Laura; Simoes, Marcus; Fernandes, Fabio; Poulsen, Steen Hvitfeldt; Diemberger, Igor; Perfetto, Federico; Solomon, Scott D.; Di Carli, Marcelo; Badri, Prajakta; White, Matthew T.; Chen, Jihong; Yureneva, Elena; Sweetser, Marianne T.; Jay, Patrick Y.; Garg, Pushkal P.; Vest, John; Gillmore, Julian D.; APOLLO-B Trial Investigators

Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy

Eplontersen用于遗传性甲状腺素蛋白淀粉样变性伴多发性神经病

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION

IF55

2023-10-1744

Coelho, Teresa; Marques, Wilson, Jr.; Dasgupta, Noel R.; Chao, Chi-Chao; Parman, Yesim; Franca, Marcondes Cavalcante, Jr.; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington

A CASE OF TRACHEOBRONCHIAL AMYLOIDOSIS

CHEST

IF8.6

2023-10-010