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H

Husain Attarwala

moderna inc
H指数:13
被引数:1,612

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Characterizing the frequency of clinical events and assessing biomarkers in propionic acidemia: a natural history study

表征临床事件发生频率并评估生物标志物在丙酸血症中的表现:一项自然病史研究

2026-03-090
OAAI
MaP NATURAL HISTORY STUDY: CLINICAL AND BIOMARKER FINDINGS IN PROPIONIC ACIDEMIA
2023-03-010
PRE
MaP NATURAL HISTORY STUDY: CLINICAL AND BIOMARKER FINDINGS IN METHYLMALONIC ACIDEMIA DUE TO MUT DEFICIENCY
2023-03-010
PRE
Impact of enhanced metabolic stability on pharmacokinetics and pharmacodynamics of GalNAc-siRNA conjugates
2017-09-15203
OAAI
An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia
2015-04-13254
PREAI