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Mark A. Kay

stanford university

112H-index
419Paper Count
5.0WCitation Count
Published Papers 240
Publication Date
lnc122 RNA prevents liver tumorigenesis in MYC-driven liver cancer
err2026-06-05
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errOAAI
errHagoon Jang; Feijie Zhang; Bo Kyoung Suh; Anh Le; Calvin J. Stephens; Kerriann M. Casey; Mark A. Kay
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First-in-human nuclease-free homologous recombination-dependent gene editing in pediatric patients with methylmalonic acidemia: results of a phase 1/2 study
err2026-03-30
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errOAAI
errJirair K. Bedoyan; Thomas Morgan; Angela Sun; Hong Li; Daniel Gruskin; Marie Payton; Frederic Chereau; Eugene Scott Swenson; Qun Lin; Mark A. Kay; Jerry Vockley
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Potential effects of endogenous RNA/DNA hybrids on CRISPR/Cas9-mediated homology-directed repair
err2026-02-27
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errOAAI
errFrancesco Puzzo; Batuhan Bayram; Claudia Macaubas; Angela Lin; Hagoon Jang; Feijie Zhang; Elizabeth Mellins; Mark A. Kay
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Stereo-random oligonucleotides enable efficient recruitment of ADAR in vitro and in vivo
err2025-10-03
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errOAAI
errLaura S. Pfeiffer; Tobias Merkle; Paul Vogel; Inga Jarmoskaite; Jonathan M. Geisinger; Ngadhnjim Latifi; Marco Herrera-Barrera; Feijie Zhang; Lisa Groß; Carolin Schlitz; Daniel T. Hofacker; Clemens Lochmann; Davide Fumagalli; Stefanie Gackstatter; Vanessa Deisling; Mark A. Kay; Jin Billy Li; Thorsten Stafforst
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Development of a novel gene editing lexicon for hemophilia: methodology and results
err2025-02-01
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errOAAI
errKessler, Craig M.; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Sindhurakar, Anil; Whyte, Lauren; Delwart, Virginie; Chiao, Megan; Gutstein, David E.; Antonino, Ilia; Hermans, Cedric; Pipe, Steven W.
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Operationalising a Haemophilia Gene Editing Lexicon for Practical Use
err2025-01-27
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PREAI
errMckeown, William; Hermans, Cedric; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Pierce, Glenn F.; Khair, Kate; Valentino, Leonard A.; Pipe, Steven W.; Pillai, Monisha; Jones, Micheala; Delwart, Virginie; Sindhurakar, Anil; Gutstein, David E.; Kessler, Craig M.
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AAV-mediated genome editing is influenced by the formation of R-loops
err2024-12-01
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PREAI
errPuzzo, Francesco; Crossley, Magdalena P.; Goswami, Aranyak; Zhang, Feijie; Pekrun, Katja; Garzon, Jada L.; Cimprich, Karlene A.; Kay, Mark A.
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A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results
err2024-10-22
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errOAAI
errHermans, Cedric; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Pipe, Steven W.; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Chiao, Megan; Antonino, Ilia; Kessler, Craig
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Correlation of antigen expression with epigenetic modifications after rAAV delivery of a human factor IX variant in mice and rhesus macaques
err2024-07-01
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PREAI
errPekrun, Katja; Stephens, Calvin J.; Gonzalez-Sandoval, Adriana; Goswami, Aranyak; Zhang, Feijie; Tarantal, Alice F.; Blouse, Grant; Kay, Mark A.
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Genome engineering with Cas9 and AAV repair templates generates frequent concatemeric insertions of viral vectors
err2024-04-08
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PREAI
errSuchy, Fabian P.; Karigane, Daiki; Nakauchi, Yusuke; Higuchi, Maimi; Zhang, Jinyu; Pekrun, Katja; Hsu, Ian; Fan, Amy C.; Nishimura, Toshinobu; Charlesworth, Carsten T.; Bhadury, Joydeep; Nishimura, Toshiya; Wilkinson, Adam C.; Kay, Mark A.; Majeti, Ravindra; Nakauchi, Hiromitsu
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The AAV capsid can influence the epigenetic marking of rAAV delivered episomal genomes in a species dependent manner
err2023-04-28
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errOAAI
errGonzalez-Sandoval, Adriana; Pekrun, Katja; Tsuji, Shinnosuke; Zhang, Feijie; Hung, King L.; Chang, Howard Y.; Kay, Mark A.
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A strategy for high antibody expression with low anti-drug antibodies using AAV9 vectors
err2023-04-21
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errOAAI
errDavis-Gardner, Meredith E.; Weber, Jesse A.; Xie, Jun; Pekrun, Katja; Alexander, Eric A.; Weisgrau, Kim L.; Furlott, Jessica R.; Rakasz, Eva G.; Kay, Mark A.; Gao, Guangping; Farzan, Michael; Gardner, Matthew R.
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Postintegrative gene silencing within the Sleeping Beauty transposition system
err2023-03-27
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errOAAI
errGarrison, Brian S.; Yant, Stephen R.; Mikkelsen, Jacob Giehrn; Kay, Mark A.
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High-resolution genome-wide mapping of transposon integration in mammals
err2023-03-27
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errOAAI
errYant, SR; Wu, XL; Huang, Y; Garrison, B; Burgess, SM; Kay, MA
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A standardized ontology for naming tRNA-derived RNAs based on molecular origin
err2023-03-03
err31
errOAAI
errHolmes, Andrew D.; Chan, Patricia P.; Chen, Qi; Ivanov, Pavel; Drouard, Laurence; Polacek, Norbert; Kay, Mark A.; Lowe, Todd M.
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Aptamer-programmable adeno-associated viral vectors as a novel platform for cell-specific gene transfer
err2023-03-01
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errOAAI
errPuzzo, Francesco; Zhang, Chuanling; Gray, Bethany Powell; Zhang, Feijie; Sullenger, Bruce A.; Kay, Mark A.
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